Detalhe da pesquisa
1.
Intracerebral Gene Therapy Using AAVrh.10-hARSA Recombinant Vector to Treat Patients with Early-Onset Forms of Metachromatic Leukodystrophy: Preclinical Feasibility and Safety Assessments in Nonhuman Primates.
Hum Gene Ther Clin Dev
; 26(2): 113-24, 2015 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-25758611
2.
Debate on Germline Gene Editing.
Hum Gene Ther Methods
; 27(4): 135-42, 2016 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-27529507