Detalhe da pesquisa
1.
AAV-mediated Gene Therapy Halts Retinal Degeneration in PDE6ß-deficient Dogs.
Mol Ther
; 24(5): 867-76, 2016 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-26857842
2.
Corrective GUSB transfer to the canine mucopolysaccharidosis VII brain.
Mol Ther
; 22(4): 762-73, 2014 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-24343103
3.
Successful gene therapy in the RPGRIP1-deficient dog: a large model of cone-rod dystrophy.
Mol Ther
; 22(2): 265-277, 2014 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-24091916
4.
Restoration of vision in the pde6ß-deficient dog, a large animal model of rod-cone dystrophy.
Mol Ther
; 20(11): 2019-30, 2012 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-22828504
5.
Efficient intracerebral delivery of AAV5 vector encoding human ARSA in non-human primate.
Hum Mol Genet
; 19(1): 147-58, 2010 Jan 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-19837699
6.
Safe, efficient, and reproducible gene therapy of the brain in the dog models of Sanfilippo and Hurler syndromes.
Mol Ther
; 19(2): 251-9, 2011 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-21139569
7.
Storage vesicles in neurons are related to Golgi complex alterations in mucopolysaccharidosis IIIB.
Am J Pathol
; 177(6): 2984-99, 2010 Dec.
Artigo
em Inglês
| MEDLINE | ID: mdl-21037080
8.
Neonatal systemic delivery of scAAV9 in rodents and large animals results in gene transfer to RPE cells in the retina.
Exp Eye Res
; 93(4): 491-502, 2011 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-21723863
9.
Intravenous administration of self-complementary AAV9 enables transgene delivery to adult motor neurons.
Mol Ther
; 17(7): 1187-96, 2009 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-19367261
10.
Lysosomal storage disease in two presumed-related springboks (Antidorcas marsupialis).
J Zoo Wildl Med
; 41(1): 104-10, 2010 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-20722261
11.
Intra-CSF AAV9 and AAVrh10 Administration in Nonhuman Primates: Promising Routes and Vectors for Which Neurological Diseases?
Mol Ther Methods Clin Dev
; 17: 771-784, 2020 Jun 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-32355866
12.
Congenital cataract in 1-day-old French Mulard ducklings.
Avian Pathol
; 38(1): 9-11, 2009 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-19130351
13.
Subretinal delivery of recombinant AAV serotype 8 vector in dogs results in gene transfer to neurons in the brain.
Mol Ther
; 16(5): 916-23, 2008 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-18388922
14.
Satellite cells fail to contribute to muscle repair but are functional in Pompe disease (glycogenosis type II).
Acta Neuropathol Commun
; 6(1): 116, 2018 10 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-30382921
15.
Primary meningeal T-cell lymphoma in a harbor seal (Phoca vitulina).
J Zoo Wildl Med
; 38(2): 323-8, 2007 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-17679518
16.
Multi-harmonic Imaging in the Second Near-Infrared Window of Nanoparticle-Labeled Stem Cells as a Monitoring Tool in Tissue Depth.
ACS Nano
; 11(7): 6672-6681, 2017 07 25.
Artigo
em Inglês
| MEDLINE | ID: mdl-28644009
17.
Vitrectomy Before Intravitreal Injection of AAV2/2 Vector Promotes Efficient Transduction of Retinal Ganglion Cells in Dogs and Nonhuman Primates.
Hum Gene Ther Methods
; 27(3): 122-34, 2016 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-27229628
18.
Intracerebral Gene Therapy Using AAVrh.10-hARSA Recombinant Vector to Treat Patients with Early-Onset Forms of Metachromatic Leukodystrophy: Preclinical Feasibility and Safety Assessments in Nonhuman Primates.
Hum Gene Ther Clin Dev
; 26(2): 113-24, 2015 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-25758611
19.
Multiple immune factors are involved in controlling acute and chronic chikungunya virus infection.
PLoS Negl Trop Dis
; 8(12): e3354, 2014 Dec.
Artigo
em Inglês
| MEDLINE | ID: mdl-25474568
20.
scAAV9 intracisternal delivery results in efficient gene transfer to the central nervous system of a feline model of motor neuron disease.
Hum Gene Ther
; 24(7): 670-82, 2013 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-23799774