Detalhe da pesquisa
1.
On- and off-target effects of paired CRISPR-Cas nickase in primary human cells.
Mol Ther
; 32(5): 1298-1310, 2024 May 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-38459694
2.
Splicing Modulation via Antisense Oligonucleotides in Recessive Dystrophic Epidermolysis Bullosa.
Int J Mol Sci
; 25(2)2024 Jan 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-38255836
3.
MicroRNA-200b-mediated reversion of a spectrum of epithelial-to-mesenchymal transition states in recessive dystrophic epidermolysis bullosa squamous cell carcinomas.
Br J Dermatol
; 190(1): 80-93, 2023 Dec 20.
Artigo
em Inglês
| MEDLINE | ID: mdl-37681509
4.
Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa.
Mol Ther
; 30(8): 2680-2692, 2022 08 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-35490295
5.
A Novel Fluorescence-Based Screen of Gene Editing Molecules for Junctional Epidermolysis Bullosa.
Int J Mol Sci
; 24(6)2023 Mar 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-36982270
6.
COL7A1 Editing via RNA Trans-Splicing in RDEB-Derived Skin Equivalents.
Int J Mol Sci
; 24(5)2023 Feb 22.
Artigo
em Inglês
| MEDLINE | ID: mdl-36901775
7.
5'RNA Trans-Splicing Repair of COL7A1 Mutant Transcripts in Epidermolysis Bullosa.
Int J Mol Sci
; 23(3)2022 Feb 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-35163654
8.
Evaluating a Targeted Cancer Therapy Approach Mediated by RNA trans-Splicing In Vitro and in a Xenograft Model for Epidermolysis Bullosa-Associated Skin Cancer.
Int J Mol Sci
; 23(1)2022 Jan 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-35008999
9.
Selective Activation of CNS and Reference PPARGC1A Promoters Is Associated with Distinct Gene Programs Relevant for Neurodegenerative Diseases.
Int J Mol Sci
; 22(7)2021 Mar 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-33804860
10.
Personalized Development of Antisense Oligonucleotides for Exon Skipping Restores Type XVII Collagen Expression in Junctional Epidermolysis Bullosa.
Int J Mol Sci
; 22(7)2021 Mar 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-33805154
11.
A cancer stem cell-like phenotype is associated with miR-10b expression in aggressive squamous cell carcinomas.
Cell Commun Signal
; 18(1): 61, 2020 04 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-32276641
12.
COL7A1 Editing via CRISPR/Cas9 in Recessive Dystrophic Epidermolysis Bullosa.
Mol Ther
; 25(11): 2573-2584, 2017 11 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-28800953
13.
Cut and Paste: Efficient Homology-Directed Repair of a Dominant Negative KRT14 Mutation via CRISPR/Cas9 Nickases.
Mol Ther
; 25(11): 2585-2598, 2017 11 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-28888469
14.
RNA Trans-Splicing Modulation via Antisense Molecule Interference.
Int J Mol Sci
; 19(3)2018 Mar 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-29518954
15.
Designing Efficient Double RNA trans-Splicing Molecules for Targeted RNA Repair.
Int J Mol Sci
; 17(10)2016 Sep 22.
Artigo
em Inglês
| MEDLINE | ID: mdl-27669223
16.
AID induces intraclonal diversity and genomic damage in CD86(+) chronic lymphocytic leukemia cells.
Eur J Immunol
; 44(12): 3747-57, 2014 Dec.
Artigo
em Inglês
| MEDLINE | ID: mdl-25179679
17.
Trans-splicing improvement by the combined application of antisense strategies.
Int J Mol Sci
; 16(1): 1179-91, 2015 Jan 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-25569093
18.
Dendritic cells activated by IFN-γ/STAT1 express IL-31 receptor and release proinflammatory mediators upon IL-31 treatment.
J Immunol
; 188(11): 5319-26, 2012 Jun 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-22539792
19.
A novel screening system improves genetic correction by internal exon replacement.
Nucleic Acids Res
; 39(16): e108, 2011 Sep 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-21685452
20.
K14 mRNA reprogramming for dominant epidermolysis bullosa simplex.
Hum Mol Genet
; 19(23): 4715-25, 2010 Dec 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-20861136