Detalhe da pesquisa
1.
Counteracting chromatin effects of a splicing-correcting antisense oligonucleotide improves its therapeutic efficacy in spinal muscular atrophy.
Cell
; 185(12): 2057-2070.e15, 2022 06 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-35688133
2.
Motor neuron cell-nonautonomous rescue of spinal muscular atrophy phenotypes in mild and severe transgenic mouse models.
Genes Dev
; 29(3): 288-97, 2015 Feb 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-25583329
3.
RNA-sequencing of a mouse-model of spinal muscular atrophy reveals tissue-wide changes in splicing of U12-dependent introns.
Nucleic Acids Res
; 45(1): 395-416, 2017 Jan 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-27557711
4.
Antisense oligonucleotide therapy for H3.3K27M diffuse midline glioma.
Sci Transl Med
; 15(691): eadd8280, 2023 04 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-37043556
5.
Effects of Dipeptidyl Peptidase-4 Inhibition with MK-0431 on Syngeneic Mouse Islet Transplantation.
Int J Endocrinol
; 2014: 795283, 2014.
Artigo
em Inglês
| MEDLINE | ID: mdl-25165473
6.
Prevention and Reversal of Diabetes by All-Trans Retinoid Acid and Exendin-4 in NOD Mice.
Int J Endocrinol
; 2014: 435481, 2014.
Artigo
em Inglês
| MEDLINE | ID: mdl-24995016
7.
Tetracyclines that promote SMN2 exon 7 splicing as therapeutics for spinal muscular atrophy.
Sci Transl Med
; 1(5): 5ra12, 2009 Nov 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-20161659