Detalhe da pesquisa
1.
A systematic capsid evolution approach performed in vivo for the design of AAV vectors with tailored properties and tropism.
Proc Natl Acad Sci U S A
; 116(52): 27053-27062, 2019 Dec 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-31818949
2.
Preclinical quality, safety, and efficacy of a human embryonic stem cell-derived product for the treatment of Parkinson's disease, STEM-PD.
Cell Stem Cell
; 30(10): 1299-1314.e9, 2023 10 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-37802036
3.
Monitoring the interactions between alpha-synuclein and Tau in vitro and in vivo using bimolecular fluorescence complementation.
Sci Rep
; 12(1): 2987, 2022 02 22.
Artigo
em Inglês
| MEDLINE | ID: mdl-35194057
4.
Grafts Derived from an α-Synuclein Triplication Patient Mediate Functional Recovery but Develop Disease-Associated Pathology in the 6-OHDA Model of Parkinson's Disease.
J Parkinsons Dis
; 11(2): 515-528, 2021.
Artigo
em Inglês
| MEDLINE | ID: mdl-33361611
5.
Transcriptional activity of novel ALDH1L1 promoters in the rat brain following AAV vector-mediated gene transfer.
Mol Ther Methods Clin Dev
; 3: 16075, 2016.
Artigo
em Inglês
| MEDLINE | ID: mdl-27990448