Detalhe da pesquisa
1.
Betibeglogene Autotemcel Gene Therapy for Non-ß0/ß0 Genotype ß-Thalassemia.
N Engl J Med
; 386(5): 415-427, 2022 02 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-34891223
2.
How I treat cytopenias after CAR T-cell therapy.
Blood
; 141(20): 2460-2469, 2023 05 18.
Artigo
em Inglês
| MEDLINE | ID: mdl-36800563
3.
Hypomethylating agents are associated with high rates of hematologic toxicity in patients with secondary myeloid neoplasms developing after acquired aplastic anemia.
Haematologica
; 2024 Apr 18.
Artigo
em Inglês
| MEDLINE | ID: mdl-38634143
4.
Inherited bone marrow failure with macrothrombocytopenia due to germline tubulin beta class I (TUBB) variant.
Br J Haematol
; 200(2): 222-228, 2023 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36207145
5.
Comparison of hematopoietic cell transplant conditioning regimens for hemophagocytic lymphohistiocytosis disorders.
J Allergy Clin Immunol
; 149(3): 1097-1104.e2, 2022 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-34375618
6.
Hematologic abnormalities in Aicardi Goutières Syndrome.
Mol Genet Metab
; 136(4): 324-329, 2022 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-35786528
7.
SLC25A38 congenital sideroblastic anemia: Phenotypes and genotypes of 31 individuals from 24 families, including 11 novel mutations, and a review of the literature.
Hum Mutat
; 42(11): 1367-1383, 2021 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-34298585
8.
Diagnostic work-up for severe aplastic anemia in children: Consensus of the North American Pediatric Aplastic Anemia Consortium.
Am J Hematol
; 96(11): 1491-1504, 2021 11 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-34342889
9.
Partially CD3+-Depleted Unrelated and Haploidentical Donor Peripheral Stem Cell Transplantation Has Favorable Graft-versus-Host Disease and Survival Rates in Pediatric Hematologic Malignancy.
Biol Blood Marrow Transplant
; 26(3): 493-501, 2020 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-31765697
10.
Diagnosis and treatment of pediatric myelodysplastic syndromes: A survey of the North American Pediatric Aplastic Anemia Consortium.
Pediatr Blood Cancer
; 67(10): e28652, 2020 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-32779892
11.
CD3+/CD19+ Depleted Matched and Mismatched Unrelated Donor Hematopoietic Stem Cell Transplant with Targeted T Cell Addback Is Associated with Excellent Outcomes in Pediatric Patients with Nonmalignant Hematologic Disorders.
Biol Blood Marrow Transplant
; 25(3): 549-555, 2019 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-30312755
12.
Immunosuppressive therapy for pediatric aplastic anemia: a North American Pediatric Aplastic Anemia Consortium study.
Haematologica
; 104(10): 1974-1983, 2019 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-30948484
13.
Development of hemolytic paroxysmal nocturnal hemoglobinuria without graft loss following hematopoietic stem cell transplantation for acquired aplastic anemia.
Pediatr Transplant
; 23(4): e13393, 2019 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-30900367
14.
Successful treatment of pulmonary mucormycosis in two pediatric hematopoietic stem cell transplant patients.
Pediatr Transplant
; 22(7): e13270, 2018 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-30014584
15.
Management of Refractory Pediatric Kaposiform Hemangioendothelioma With Sirolimus and Aspirin.
J Pediatr Hematol Oncol
; 40(4): e239-e242, 2018 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-29240034
16.
Recent advances in understanding clonal haematopoiesis in aplastic anaemia.
Br J Haematol
; 177(4): 509-525, 2017 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-28107566
17.
Paediatric severe aplastic anaemia treatment: where to start?
Br J Haematol
; 192(3): 417-419, 2021 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-33400262
18.
Heparan sulfate: a stem cell therapy target?
Blood
; 124(19): 2895-6, 2014 Nov 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-25377556
19.
Disrupted lymphocyte homeostasis in hepatitis-associated acquired aplastic anemia is associated with short telomeres.
Am J Hematol
; 91(2): 243-7, 2016 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-26615915
20.
Megakaryocytes promote murine osteoblastic HSC niche expansion and stem cell engraftment after radioablative conditioning.
Blood
; 121(26): 5238-49, 2013 Jun 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-23667055