Pesquisa | BVS Doenças Infecciosas e Parasitárias

1.

CRISPR-Cas9 Gene Editing for Sickle Cell Disease and ß-Thalassemia.

Frangoul, Haydar; Altshuler, David; Cappellini, M Domenica; Chen, Yi-Shan; Domm, Jennifer; Eustace, Brenda K; Foell, Juergen; de la Fuente, Josu; Grupp, Stephan; Handgretinger, Rupert; Ho, Tony W; Kattamis, Antonis; Kernytsky, Andrew; Lekstrom-Himes, Julie; Li, Amanda M; Locatelli, Franco; Mapara, Markus Y; de Montalembert, Mariane; Rondelli, Damiano; Sharma, Akshay; Sheth, Sujit; Soni, Sandeep; Steinberg, Martin H; Wall, Donna; Yen, Angela; Corbacioglu, Selim.

N Engl J Med ; 384(3): 252-260, 2021 01 21.

Artigo em Inglês | MEDLINE | ID: mdl-33283989

2.

Spin device-based image edge detection architecture for neuromorphic computing.

Verma, Gaurav; Soni, Sandeep; Kaushik, Brajesh Kumar.

Nanotechnology ; 35(5)2023 Nov 15.

Artigo em Inglês | MEDLINE | ID: mdl-37797609

3.

Gene Therapy in Patients with Transfusion-Dependent ß-Thalassemia.

Thompson, Alexis A; Walters, Mark C; Kwiatkowski, Janet; Rasko, John E J; Ribeil, Jean-Antoine; Hongeng, Suradej; Magrin, Elisa; Schiller, Gary J; Payen, Emmanuel; Semeraro, Michaela; Moshous, Despina; Lefrere, Francois; Puy, Hervé; Bourget, Philippe; Magnani, Alessandra; Caccavelli, Laure; Diana, Jean-Sébastien; Suarez, Felipe; Monpoux, Fabrice; Brousse, Valentine; Poirot, Catherine; Brouzes, Chantal; Meritet, Jean-François; Pondarré, Corinne; Beuzard, Yves; Chrétien, Stany; Lefebvre, Thibaud; Teachey, David T; Anurathapan, Usanarat; Ho, P Joy; von Kalle, Christof; Kletzel, Morris; Vichinsky, Elliott; Soni, Sandeep; Veres, Gabor; Negre, Olivier; Ross, Robert W; Davidson, David; Petrusich, Alexandria; Sandler, Laura; Asmal, Mohammed; Hermine, Olivier; De Montalembert, Mariane; Hacein-Bey-Abina, Salima; Blanche, Stéphane; Leboulch, Philippe; Cavazzana, Marina.

N Engl J Med ; 378(16): 1479-1493, 2018 04 19.

Artigo em Inglês | MEDLINE | ID: mdl-29669226

4.

A Phase 2 Trial of KIR-Mismatched Unrelated Donor Transplantation Using in Vivo T Cell Depletion with Antithymocyte Globulin in Acute Myelogenous Leukemia: Children's Oncology Group AAML05P1 Study.

Davies, Stella M; Iannone, Robert; Alonzo, Todd A; Wang, Yi-Cheng; Gerbing, Robert; Soni, Sandeep; Kolb, E Anders; Meshinchi, Soheil; Orchard, Paul J; Burns, Linda J; Shenoy, Shalini; Leung, Wing.

Biol Blood Marrow Transplant ; 26(4): 712-717, 2020 04.

Artigo em Inglês | MEDLINE | ID: mdl-31870931

5.

Gene Therapy in a Patient with Sickle Cell Disease.

Ribeil, Jean-Antoine; Hacein-Bey-Abina, Salima; Payen, Emmanuel; Magnani, Alessandra; Semeraro, Michaela; Magrin, Elisa; Caccavelli, Laure; Neven, Benedicte; Bourget, Philippe; El Nemer, Wassim; Bartolucci, Pablo; Weber, Leslie; Puy, Hervé; Meritet, Jean-François; Grevent, David; Beuzard, Yves; Chrétien, Stany; Lefebvre, Thibaud; Ross, Robert W; Negre, Olivier; Veres, Gabor; Sandler, Laura; Soni, Sandeep; de Montalembert, Mariane; Blanche, Stéphane; Leboulch, Philippe; Cavazzana, Marina.

N Engl J Med ; 376(9): 848-855, 2017 03 02.

Artigo em Inglês | MEDLINE | ID: mdl-28249145

6.

Gene therapies for transfusion dependent ß-thalassemia: Current status and critical criteria for success.

Soni, Sandeep.

Am J Hematol ; 95(9): 1099-1112, 2020 09.

Artigo em Inglês | MEDLINE | ID: mdl-32562290

7.

Chemistry, manufacturing and controls for gene modified hematopoietic stem cells.

Soni, Sandeep; Kohn, Donald B.

Cytotherapy ; 21(3): 358-366, 2019 03.

Artigo em Inglês | MEDLINE | ID: mdl-30745225

8.

Outcomes of Unrelated Donor Stem Cell Transplantion with Post-Transplant Cyclophosphamide for Graft-versus-Host Disease Prophylaxis in Patients with Severe Sickle Cell Disease.

Rangarajan, Hemalatha G; Abu-Arja, Rolla; Pai, Vinita; Guilcher, Gregory M T; Soni, Sandeep.

Biol Blood Marrow Transplant ; 24(2): 413-417, 2018 02.

Artigo em Inglês | MEDLINE | ID: mdl-29061531

9.

Unrelated Donor Transplantation in Children with Thalassemia using Reduced-Intensity Conditioning: The URTH Trial.

Shenoy, Shalini; Walters, Mark C; Ngwube, Alex; Soni, Sandeep; Jacobsohn, David; Chaudhury, Sonali; Grimley, Michael; Chan, Kawah; Haight, Ann; Kasow, Kimberley A; Parikh, Suhag; Andreansky, Martin; Connelly, Jim; Delgado, David; Godder, Kamar; Hale, Gregory; Nieder, Michael; Pulsipher, Michael A; Trachtenberg, Felicia; Neufeld, Ellis; Kwiatkowski, Janet L; Thompson, Alexis A.

Biol Blood Marrow Transplant ; 24(6): 1216-1222, 2018 06.

Artigo em Inglês | MEDLINE | ID: mdl-29374585

10.

2023 Gene Therapy Mini-Series.

Soni, Sandeep.

Cytotherapy ; 25(3): 229, 2023 03.

Artigo em Inglês | MEDLINE | ID: mdl-36725443

11.

Phase I Study of Clofarabine and 2-Gy Total Body Irradiation as a Nonmyeloablative Preparative Regimen for Hematopoietic Stem Cell Transplantation in Pediatric Patients with Hematologic Malignancies: A Therapeutic Advances in Childhood Leukemia Consortium Study.

Soni, Sandeep; Abdel-Azim, Hisham; McManus, Meghann; Nemecek, Eneida; Sposto, Richard; Woolfrey, Ann; Frangoul, Haydar.

Biol Blood Marrow Transplant ; 23(7): 1134-1141, 2017 Jul.

Artigo em Inglês | MEDLINE | ID: mdl-28396162

12.

Preclinical safety evaluation of submicronized sildenafil citrate nebulization solution in small experimental animals.

Agrawal, Priyanka; Soni, Sandeep; Mittal, Gaurav; Bhatnagar, Aseem.

Exp Lung Res ; 41(8): 450-8, 2015.

Artigo em Inglês | MEDLINE | ID: mdl-26381717

13.

Development and Optimization of Gastro-Retentive Controlled-Release Tablet of Calcium-Disodium Edentate and its In Vivo Gamma Scintigraphic Evaluation.

Kumar, Neeraj; Soni, Sandeep; Singh, Thakuri; Kumar, Amit; Ahmad, Farhan Jalees; Bhatnagar, Aseem; Mittal, Gaurav.

AAPS PharmSciTech ; 16(6): 1270-80, 2015 Dec.

Artigo em Inglês | MEDLINE | ID: mdl-25771737

14.

Combined umbilical cord blood and bone marrow from HLA-identical sibling donors for hematopoietic stem cell transplantation in children with hemoglobinopathies.

Soni, Sandeep; Boulad, Farid; Cowan, Morton J; Scaradavou, Andromachi; Dahake, Jueeli; Edwards, Sandie; Walters, Mark C.

Pediatr Blood Cancer ; 61(9): 1690-4, 2014 Sep.

Artigo em Inglês | MEDLINE | ID: mdl-24803091

15.

Outcomes of matched sibling donor hematopoietic stem cell transplantation for severe sickle cell disease with myeloablative conditioning and intermediate-dose of rabbit anti-thymocyte globulin.

Soni, Sandeep; Gross, Thomas G; Rangarajan, Hemalatha; Baker, K Scott; Sturm, Mollie; Rhodes, Melissa.

Pediatr Blood Cancer ; 61(9): 1685-9, 2014 Sep.

Artigo em Inglês | MEDLINE | ID: mdl-24740582

16.

Successful unrelated umbilical cord blood transplantation for class 3 ß-thalassemia major using a reduced-toxicity regimen.

Soni, Sandeep; Breslin, Nancy; Cheerva, Alexandra.

Pediatr Transplant ; 18(2): E41-3, 2014 Mar.

Artigo em Inglês | MEDLINE | ID: mdl-24330091

17.

Busulfan and melphalan as consolidation therapy with autologous peripheral blood stem cell transplantation following Children's Oncology Group (COG) induction platform for high-risk neuroblastoma: early results from a single institution.

Soni, Sandeep; Pai, Vinita; Gross, Thomas G; Ranalli, Mark.

Pediatr Transplant ; 18(2): 217-20, 2014 Mar.

Artigo em Inglês | MEDLINE | ID: mdl-24341617

18.

Levetiracetam for busulfan-induced seizure prophylaxis in children undergoing hematopoietic stem cell transplantation.

Soni, Sandeep; Skeens, Micah; Termuhlen, Amanda M; Bajwa, Rajinder P S; Gross, Thomas G; Pai, Vinita.

Pediatr Blood Cancer ; 59(4): 762-4, 2012 Oct.

Artigo em Inglês | MEDLINE | ID: mdl-22378696

19.

Metabolic syndrome and endocrine dysfunctions after HSCT in children.

Bajwa, Rajinder; Skeens, Micah; Garee, Amy; Miao, Yongjie; Soni, Sandeep; Pietryga, Daniel; Gross, Thomas; Termuhlen, Amanda.

Pediatr Transplant ; 16(8): 872-8, 2012 Dec.

Artigo em Inglês | MEDLINE | ID: mdl-23131056

20.

Disseminated Rhizomucor pusillus causing early multiorgan failure during hematopoietic stem cell transplantation for severe aplastic anemia.

Rawlinson, Neil J; Fung, Bonita; Gross, Thomas G; Termuhlen, Amanda M; Skeens, Micah; Garee, Amy; Soni, Sandeep; Pietryga, Daniel; Bajwa, Rajinder P S.

J Pediatr Hematol Oncol ; 33(3): 235-7, 2011 Apr.

Artigo em Inglês | MEDLINE | ID: mdl-21358340

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