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An AAVS1-targeted minigene platform for correction of iPSCs from all five types of chronic granulomatous disease.
Merling, Randall K; Sweeney, Colin L; Chu, Jessica; Bodansky, Aaron; Choi, Uimook; Priel, Debra Long; Kuhns, Douglas B; Wang, Hongmei; Vasilevsky, Sam; De Ravin, Suk See; Winkler, Thomas; Dunbar, Cynthia E; Zou, Jizhong; Zarember, Kol A; Gallin, John I; Holland, Steven M; Malech, Harry L.
Afiliação
  • Merling RK; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
  • Sweeney CL; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
  • Chu J; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
  • Bodansky A; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
  • Choi U; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
  • Priel DL; Neutrophil Monitoring Lab, Applied/Developmental Research Directorate, Frederick National Laboratory for Cancer Research, Frederick, Maryland, USA.
  • Kuhns DB; Neutrophil Monitoring Lab, Applied/Developmental Research Directorate, Frederick National Laboratory for Cancer Research, Frederick, Maryland, USA.
  • Wang H; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
  • Vasilevsky S; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
  • De Ravin SS; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
  • Winkler T; Hematology Branch, National Heart, Lung, and Blood Institute, NIH, Bethesda, Maryland, USA.
  • Dunbar CE; Hematology Branch, National Heart, Lung, and Blood Institute, NIH, Bethesda, Maryland, USA.
  • Zou J; Center for Regenerative Medicine, National Institute of Arthritis and Musculoskeletal and Skin Diseases, NIH, Bethesda, Maryland, USA.
  • Zarember KA; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
  • Gallin JI; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
  • Holland SM; Laboratory of Clinical Infectious Diseases, NIAID, NIH, Bethesda, Maryland, USA.
  • Malech HL; Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases (NIAID), National Institutes of Health (NIH), Bethesda, Maryland, USA.
Mol Ther ; 23(1): 147-57, 2015 Jan.
Article em En | MEDLINE | ID: mdl-25288370

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Células-Tronco Hematopoéticas / Dependovirus / NADPH Oxidases / Células-Tronco Pluripotentes Induzidas / Doença Granulomatosa Crônica Limite: Humans Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2015 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Células-Tronco Hematopoéticas / Dependovirus / NADPH Oxidases / Células-Tronco Pluripotentes Induzidas / Doença Granulomatosa Crônica Limite: Humans Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2015 Tipo de documento: Article País de afiliação: Estados Unidos