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An RNAi therapeutic targeting antithrombin to rebalance the coagulation system and promote hemostasis in hemophilia.
Sehgal, Alfica; Barros, Scott; Ivanciu, Lacramioara; Cooley, Brian; Qin, June; Racie, Tim; Hettinger, Julia; Carioto, Mary; Jiang, Yongfeng; Brodsky, Josh; Prabhala, Harsha; Zhang, Xuemei; Attarwala, Husain; Hutabarat, Renta; Foster, Don; Milstein, Stuart; Charisse, Klaus; Kuchimanchi, Satya; Maier, Martin A; Nechev, Lubo; Kandasamy, Pachamuthu; Kel'in, Alexander V; Nair, Jayaprakash K; Rajeev, Kallanthottathil G; Manoharan, Muthiah; Meyers, Rachel; Sorensen, Benny; Simon, Amy R; Dargaud, Yesim; Negrier, Claude; Camire, Rodney M; Akinc, Akin.
Afiliação
  • Sehgal A; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Barros S; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Ivanciu L; Division of Hematology, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.
  • Cooley B; Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel Hill, North Carolina, USA. .
  • Qin J; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Racie T; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Hettinger J; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Carioto M; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Jiang Y; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Brodsky J; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Prabhala H; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Zhang X; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Attarwala H; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Hutabarat R; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Foster D; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Milstein S; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Charisse K; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Kuchimanchi S; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Maier MA; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Nechev L; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Kandasamy P; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Kel'in AV; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Nair JK; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Rajeev KG; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Manoharan M; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Meyers R; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Sorensen B; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Simon AR; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Dargaud Y; Unité d'Hémostase Clinique, Hôpital Edouard Herriot, Université Lyon 1, Lyon, France.
  • Negrier C; Unité d'Hémostase Clinique, Hôpital Edouard Herriot, Université Lyon 1, Lyon, France.
  • Camire RM; Division of Hematology, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.
  • Akinc A; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
Nat Med ; 21(5): 492-7, 2015 May.
Article em En | MEDLINE | ID: mdl-25849132

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Coagulação Sanguínea / Fator IX / Fator VIII / Antitrombinas / Interferência de RNA / Hemofilia A Tipo de estudo: Prognostic_studies Limite: Animals / Female / Humans / Male Idioma: En Revista: Nat Med Assunto da revista: BIOLOGIA MOLECULAR / MEDICINA Ano de publicação: 2015 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Coagulação Sanguínea / Fator IX / Fator VIII / Antitrombinas / Interferência de RNA / Hemofilia A Tipo de estudo: Prognostic_studies Limite: Animals / Female / Humans / Male Idioma: En Revista: Nat Med Assunto da revista: BIOLOGIA MOLECULAR / MEDICINA Ano de publicação: 2015 Tipo de documento: Article País de afiliação: Estados Unidos