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Effects of Lumacaftor-Ivacaftor Therapy on Cystic Fibrosis Transmembrane Conductance Regulator Function in Phe508del Homozygous Patients with Cystic Fibrosis.
Graeber, Simon Y; Dopfer, Christian; Naehrlich, Lutz; Gyulumyan, Lena; Scheuermann, Heike; Hirtz, Stephanie; Wege, Sabine; Mairbäurl, Heimo; Dorda, Marie; Hyde, Rebecca; Bagheri-Hanson, Azadeh; Rueckes-Nilges, Claudia; Fischer, Sebastian; Mall, Marcus A; Tümmler, Burkhard.
Afiliação
  • Graeber SY; 1 Department of Translational Pulmonology.
  • Dopfer C; 2 Division of Pediatric Pulmonology and Allergy and Cystic Fibrosis Center, Department of Pediatrics, and.
  • Naehrlich L; 3 Translational Lung Research Center Heidelberg, German Center for Lung Research, University of Heidelberg, Heidelberg, Germany.
  • Gyulumyan L; 4 Department of Pediatric Pulmonology and Immunology and Cystic Fibrosis Center, Charité-Universitätsmedizin Berlin, Berlin, Germany.
  • Scheuermann H; 5 Clinic of Pediatric Pneumology, Allergology, and Neonatology and.
  • Hirtz S; 6 Biomedical Research in Endstage and Obstructive Lung Disease Hannover, German Center for Lung Research, Hannover Medical School, Hannover, Germany.
  • Wege S; 7 Department of Pediatrics, Justus-Liebig-University Giessen, Giessen, Germany.
  • Mairbäurl H; 8 Universities of Giessen and Marburg Lung Center, German Center for Lung Research, Giessen, Germany.
  • Dorda M; 5 Clinic of Pediatric Pneumology, Allergology, and Neonatology and.
  • Hyde R; 1 Department of Translational Pulmonology.
  • Bagheri-Hanson A; 1 Department of Translational Pulmonology.
  • Rueckes-Nilges C; 9 Department of Pneumology and Respiratory Critical Care Medicine, Thoraxklinik, University Hospital Heidelberg, Heidelberg, Germany; and.
  • Fischer S; 3 Translational Lung Research Center Heidelberg, German Center for Lung Research, University of Heidelberg, Heidelberg, Germany.
  • Mall MA; 9 Department of Pneumology and Respiratory Critical Care Medicine, Thoraxklinik, University Hospital Heidelberg, Heidelberg, Germany; and.
  • Tümmler B; 10 Medical Clinic VII, Sports Medicine, Heidelberg University Hospital, Heidelberg, Germany.
Am J Respir Crit Care Med ; 197(11): 1433-1442, 2018 06 01.
Article em En | MEDLINE | ID: mdl-29327948

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Biomarcadores / Quinolonas / Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística / Benzodioxóis / Agonistas dos Canais de Cloreto / Aminofenóis / Aminopiridinas Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Female / Humans / Male País/Região como assunto: Europa Idioma: En Revista: Am J Respir Crit Care Med Assunto da revista: TERAPIA INTENSIVA Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Biomarcadores / Quinolonas / Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística / Benzodioxóis / Agonistas dos Canais de Cloreto / Aminofenóis / Aminopiridinas Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Female / Humans / Male País/Região como assunto: Europa Idioma: En Revista: Am J Respir Crit Care Med Assunto da revista: TERAPIA INTENSIVA Ano de publicação: 2018 Tipo de documento: Article