Your browser doesn't support javascript.
loading
Translating SOD1 Gene Silencing toward the Clinic: A Highly Efficacious, Off-Target-free, and Biomarker-Supported Strategy for fALS.
Iannitti, Tommaso; Scarrott, Joseph M; Likhite, Shibi; Coldicott, Ian R P; Lewis, Katherine E; Heath, Paul R; Higginbottom, Adrian; Myszczynska, Monika A; Milo, Marta; Hautbergue, Guillaume M; Meyer, Kathrin; Kaspar, Brian K; Ferraiuolo, Laura; Shaw, Pamela J; Azzouz, Mimoun.
Afiliação
  • Iannitti T; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK.
  • Scarrott JM; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK.
  • Likhite S; Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH, USA; Department of Pediatrics, College of Medicine and Public Health, The Ohio State University, Columbus, OH, USA.
  • Coldicott IRP; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK.
  • Lewis KE; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK.
  • Heath PR; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK.
  • Higginbottom A; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK.
  • Myszczynska MA; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK.
  • Milo M; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK.
  • Hautbergue GM; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK.
  • Meyer K; Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH, USA; Department of Pediatrics, College of Medicine and Public Health, The Ohio State University, Columbus, OH, USA.
  • Kaspar BK; Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH, USA; Department of Pediatrics, College of Medicine and Public Health, The Ohio State University, Columbus, OH, USA; Department of Neuroscience, The Ohio State University, Columbus, OH, USA.
  • Ferraiuolo L; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK.
  • Shaw PJ; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK. Electronic address: pamela.shaw@sheffield.ac.uk.
  • Azzouz M; University of Sheffield, Sheffield Institute for Translational Neuroscience (SITraN), Department of Neuroscience, Sheffield, UK. Electronic address: m.azzouz@sheffield.ac.uk.
Mol Ther Nucleic Acids ; 12: 75-88, 2018 Sep 07.
Article em En | MEDLINE | ID: mdl-30195799

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Reino Unido