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Liver-directed gene therapy results in long-term correction of progressive familial intrahepatic cholestasis type 3 in mice.
Aronson, Sem J; Bakker, Robert S; Shi, Xiaoxia; Duijst, Suzanne; Ten Bloemendaal, Lysbeth; de Waart, Dirk R; Verheij, Joanne; Ronzitti, Giuseppe; Oude Elferink, Ronald P; Beuers, Ulrich; Paulusma, Coen C; Bosma, Piter J.
Afiliação
  • Aronson SJ; Amsterdam University Medical Centers, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, Amsterdam Gastroenterology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands.
  • Bakker RS; Amsterdam University Medical Centers, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, Amsterdam Gastroenterology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands.
  • Shi X; Amsterdam University Medical Centers, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, Amsterdam Gastroenterology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands.
  • Duijst S; Amsterdam University Medical Centers, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, Amsterdam Gastroenterology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands.
  • Ten Bloemendaal L; Amsterdam University Medical Centers, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, Amsterdam Gastroenterology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands.
  • de Waart DR; Amsterdam University Medical Centers, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, Amsterdam Gastroenterology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands.
  • Verheij J; Amsterdam University Medical Centers, University of Amsterdam, Department of Pathology, Meibergdreef 9, Amsterdam, The Netherlands.
  • Ronzitti G; INTEGRARE, Genethon, INSERM, University of Evry, University Paris-Saclay, 91002 Evry, France.
  • Oude Elferink RP; Amsterdam University Medical Centers, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, Amsterdam Gastroenterology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands.
  • Beuers U; Amsterdam University Medical Centers, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, Amsterdam Gastroenterology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands.
  • Paulusma CC; Amsterdam University Medical Centers, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, Amsterdam Gastroenterology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands.
  • Bosma PJ; Amsterdam University Medical Centers, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, Amsterdam Gastroenterology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands. Electronic address: p.j.bosma@amc.uva.nl.
J Hepatol ; 71(1): 153-162, 2019 07.
Article em En | MEDLINE | ID: mdl-30935993

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Fosfolipídeos / Bile / Terapia Genética / Colestase Intra-Hepática / Subfamília B de Transportador de Cassetes de Ligação de ATP / Cirrose Hepática Limite: Animals Idioma: En Revista: J Hepatol Assunto da revista: GASTROENTEROLOGIA Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Holanda

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Fosfolipídeos / Bile / Terapia Genética / Colestase Intra-Hepática / Subfamília B de Transportador de Cassetes de Ligação de ATP / Cirrose Hepática Limite: Animals Idioma: En Revista: J Hepatol Assunto da revista: GASTROENTEROLOGIA Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Holanda