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Real-Life Safety and Effectiveness of Lumacaftor-Ivacaftor in Patients with Cystic Fibrosis.
Burgel, Pierre-Régis; Munck, Anne; Durieu, Isabelle; Chiron, Raphaël; Mely, Laurent; Prevotat, Anne; Murris-Espin, Marlene; Porzio, Michele; Abely, Michel; Reix, Philippe; Marguet, Christophe; Macey, Julie; Sermet-Gaudelus, Isabelle; Corvol, Harriet; Bui, Stéphanie; Lemonnier, Lydie; Dehillotte, Clémence; Da Silva, Jennifer; Paillasseur, Jean-Louis; Hubert, Dominique.
Afiliação
  • Burgel PR; Université de Paris, Institut Cochin, INSERM U1016, Paris, France.
  • Munck A; Respiratory Medicine and National Reference Cystic Fibrosis Reference Center, Cochin Hospital, Assistance Publique-Hôpitaux de Paris (AP-HP), Paris, France.
  • Durieu I; ERN-Lung CF Network.
  • Chiron R; Hôpital Robert Debré, AP-HP, Paris, France.
  • Mely L; ERN-Lung CF Network.
  • Prevotat A; Centre de Référence Adulte de la Mucoviscidose, Service de Médecine Interne, Hospices Civils de Lyon, Pierre Bénite, France.
  • Murris-Espin M; Université de Lyon, Équipe d'Accueil Health Services and Performance Research (HESPER) 7425, Lyon, France.
  • Porzio M; Cystic Fibrosis Center, Hôpital Arnaud de Villeneuve, Centre Hospitalier Universitaire de Montpellier, Université de Montpellier, Montpellier, France.
  • Abely M; Hôpital Renée Sabran, Cystic Fibrosis Center, Giens, France.
  • Reix P; CHU-Lille, Cystic Fibrosis Center, Service de Pneumologie et Immuno-allergologie, Hôpital Calmette and Université de Lille, Lille, France.
  • Marguet C; Cystic Fibrosis Center, Service de Pneumologie, Pôle des Voies Respiratoires, Hôpital Larrey, CHU de Toulouse, Toulouse, France.
  • Macey J; Department of Respiratory Medicine and Cystic Fibrosis Center, Federation of Translational Medicine of Strasbourg, University Hospitals, Strasbourg, France.
  • Sermet-Gaudelus I; Department of Pediatrics A and Cystic Fibrosis Center, American Memorial Hospital, Reims, France.
  • Corvol H; UMR 5558 CNRS, Equipe EMET, Université Claude Bernard Lyon 1, Lyon, France.
  • Bui S; Cystic Fibrosis Center, Hospices Civils de Lyon, Lyon, France.
  • Lemonnier L; Pediatric Respiratory Disease and Cystic Fibrosis Center, Hospital, UNIROUEN, INSERM EA 2656, Rouen University Hospital, Université de Normandie, Rouen, France.
  • Dehillotte C; Respiratory Medicine and Cystic Fibrosis Center, CHU de Bordeaux, Bordeaux, France.
  • Da Silva J; ERN-Lung CF Network.
  • Paillasseur JL; Pediatric Respiratory Disease and Cystic Fibrosis Center, National Reference Cystic Fibrosis Reference Center, Hôpital Necker Enfants Malades, Paris France.
  • Hubert D; INSERM U 1151, Institut Necker Enfants Malades, Paris, France.
Am J Respir Crit Care Med ; 201(2): 188-197, 2020 01 15.
Article em En | MEDLINE | ID: mdl-31601120

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Estado Nutricional / Quinolonas / Fibrose Cística / Benzodioxóis / Aminofenóis / Aminopiridinas / Antibacterianos Tipo de estudo: Guideline / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Female / Humans / Male País/Região como assunto: Europa Idioma: En Revista: Am J Respir Crit Care Med Assunto da revista: TERAPIA INTENSIVA Ano de publicação: 2020 Tipo de documento: Article País de afiliação: França

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Estado Nutricional / Quinolonas / Fibrose Cística / Benzodioxóis / Aminofenóis / Aminopiridinas / Antibacterianos Tipo de estudo: Guideline / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Female / Humans / Male País/Região como assunto: Europa Idioma: En Revista: Am J Respir Crit Care Med Assunto da revista: TERAPIA INTENSIVA Ano de publicação: 2020 Tipo de documento: Article País de afiliação: França