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The long-acting C5 inhibitor, Ravulizumab, is effective and safe in adult patients with atypical hemolytic uremic syndrome naïve to complement inhibitor treatment.
Rondeau, Eric; Scully, Marie; Ariceta, Gema; Barbour, Tom; Cataland, Spero; Heyne, Nils; Miyakawa, Yoshitaka; Ortiz, Stephan; Swenson, Eugene; Vallee, Marc; Yoon, Sung-Soo; Kavanagh, David; Haller, Hermann.
Afiliação
  • Rondeau E; Intensive Care Nephrology and Transplantation Department, Assistance Publique, Hôpitaux de Paris 6, Sorbonne Université, Paris, France. Electronic address: eric.rondeau@aphp.fr.
  • Scully M; Department of Haematology, University College London Hospitals (UCLH) and Cardio-metabolic Programme, National Institute for Health Research UCLH/UC Biomedical Research Centre, London, UK.
  • Ariceta G; Paediatric Nephrology Department, University Hospital Vall d'Hebron, Barcelona, Spain.
  • Barbour T; Kidney Care, Royal Melbourne Hospital, Melbourne, Australia.
  • Cataland S; Division of Hematology, The Ohio State University Medical Center, Columbus, Ohio, USA.
  • Heyne N; Department of Kidney and Hypertension Diseases, University Hospital Tübingen, Tübingen, Germany.
  • Miyakawa Y; Department of General Internal Medicine, Saitama Medical University, Iruma, Japan.
  • Ortiz S; Clinical Pharmacology, Alexion Pharmaceutical, Inc., Boston, Massachusetts, USA.
  • Swenson E; Clinical Development, Alexion Pharmaceutical, Inc., Boston, Massachusetts, USA.
  • Vallee M; Biostatistics, Alexion Pharmaceutical, Inc., Boston, Massachusetts, USA.
  • Yoon SS; Department of Internal Medicine, Seoul National University Hospital, Seoul, Republic of Korea.
  • Kavanagh D; National Renal Complement Therapeutics Centre, Royal Victoria Hospital, Newcastle University, Newcastle upon Tyne, UK.
  • Haller H; Department of Nephrology and Hypertension, Hannover Medical School, Hannover, Germany.
Kidney Int ; 97(6): 1287-1296, 2020 06.
Article em En | MEDLINE | ID: mdl-32299680

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Microangiopatias Trombóticas / Síndrome Hemolítico-Urêmica Atípica Tipo de estudo: Diagnostic_studies Limite: Adult / Humans Idioma: En Revista: Kidney Int Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Microangiopatias Trombóticas / Síndrome Hemolítico-Urêmica Atípica Tipo de estudo: Diagnostic_studies Limite: Adult / Humans Idioma: En Revista: Kidney Int Ano de publicação: 2020 Tipo de documento: Article