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Study protocol of RESCUE-ALS: A Phase 2, randomised, double-blind, placebo-controlled study in early symptomatic amyotrophic lateral sclerosis patients to assess bioenergetic catalysis with CNM-Au8 as a mechanism to slow disease progression.
Vucic, Steve; Kiernan, Matthew C; Menon, Parvathi; Huynh, William; Rynders, Austin; Ho, Karen S; Glanzman, Robert; Hotchkin, Michael T.
Afiliação
  • Vucic S; Department of Neurology, Westmead Hospital and Western Clinical School, University of Sydney, Sydney, New South Wales, Australia.
  • Kiernan MC; Brain and Mind Centre, University of Sydney, Sydney, New South Wales, Australia.
  • Menon P; Department of Neurology, Royal Prince Alfred Hospital, Sydney, New South Wales, Australia.
  • Huynh W; Department of Neurology, Westmead Hospital and Western Clinical School, University of Sydney, Sydney, New South Wales, Australia.
  • Rynders A; Brain and Mind Centre, University of Sydney, Sydney, New South Wales, Australia.
  • Ho KS; Prince of Wales Clinical School, University of New South Wales, Sydney, New South Wales, Australia.
  • Glanzman R; Clene Nanomedicine, Salt Lake City, Utah, USA.
  • Hotchkin MT; Clene Nanomedicine, Salt Lake City, Utah, USA.
BMJ Open ; 11(1): e041479, 2021 01 11.
Article em En | MEDLINE | ID: mdl-33431491

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Esclerose Lateral Amiotrófica Tipo de estudo: Clinical_trials Limite: Adult / Humans País/Região como assunto: America do norte / Europa / Oceania Idioma: En Revista: BMJ Open Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Austrália

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Esclerose Lateral Amiotrófica Tipo de estudo: Clinical_trials Limite: Adult / Humans País/Região como assunto: America do norte / Europa / Oceania Idioma: En Revista: BMJ Open Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Austrália