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PHYOX2: a pivotal randomized study of nedosiran in primary hyperoxaluria type 1 or 2.
Baum, Michelle A; Langman, Craig; Cochat, Pierre; Lieske, John C; Moochhala, Shabbir H; Hamamoto, Shuzo; Satoh, Hiroyuki; Mourani, Chebl; Ariceta, Gema; Torres, Armando; Wolley, Martin; Belostotsky, Vladimir; Forbes, Thomas A; Groothoff, Jaap; Hayes, Wesley; Tönshoff, Burkhard; Takayama, Tatsuya; Rosskamp, Ralf; Russell, Kerry; Zhou, Jing; Amrite, Aniruddha; Hoppe, Bernd.
Afiliação
  • Baum MA; Division of Nephrology, Boston Children's Hospital, Boston, Massachusetts, USA.
  • Langman C; Department of Pediatrics, Northwestern University Feinberg School of Medicine, Chicago, Illinois, USA.
  • Cochat P; Reference Centre for Rare Renal Diseases, Hôpital Femme Mère Enfant, Lyon, France.
  • Lieske JC; Division of Nephrology and Hypertension, Mayo Clinic, Rochester, Minnesota, USA.
  • Moochhala SH; UCL Department of Renal Medicine, Royal Free Hospital, London, UK.
  • Hamamoto S; Department of Nephro-urology, Nagoya City University, Nagoya, Japan.
  • Satoh H; Department of Urology, Tokyo Metropolitan Children's Hospital, Tokyo, Japan.
  • Mourani C; Pediatrics, Hôtel Dieu de France, Beirut, Lebanon.
  • Ariceta G; Pediatric Nephrology, University Hospital Vall d'Hebron, Barcelona, Spain.
  • Torres A; Nephrology Department, Hospital Universitario de Canarias (ULL), Santa Cruz de Tenerife, Spain; Instituto Tecnologías Biomédicas (ITB), Universidad de La Laguna, Santa Cruz de Tenerife, Spain.
  • Wolley M; Kidney Health Service, Royal Brisbane and Women's Hospital, Herston, Australia.
  • Belostotsky V; Department of Pediatrics, McMaster Children's Hospital, Hamilton, Canada.
  • Forbes TA; Pediatric Nephrology, The Royal Children's Hospital, Melbourne, Australia; Department of Pediatrics, Murdoch Children's Research Institute, Melbourne, Australia.
  • Groothoff J; Department of Pediatric Nephrology, Academic Medical Center (AMC), Amsterdam, the Netherlands.
  • Hayes W; Department of Pediatric Nephrology, Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.
  • Tönshoff B; Department of Pediatrics, University Children's Hospital, Heidelberg, Germany.
  • Takayama T; Department of Urology, Jichi Medical University, Shimotsuke, Tochigi, Japan.
  • Rosskamp R; Clinical Development, Dicerna Pharmaceuticals, Inc., Lexington, Massachusetts, USA.
  • Russell K; Clinical Development, Dicerna Pharmaceuticals, Inc., Lexington, Massachusetts, USA.
  • Zhou J; Clinical Development, Dicerna Pharmaceuticals, Inc., Lexington, Massachusetts, USA.
  • Amrite A; Clinical Development, Dicerna Pharmaceuticals, Inc., Lexington, Massachusetts, USA.
  • Hoppe B; Clinical Development, Dicerna Pharmaceuticals, Inc., Lexington, Massachusetts, USA; Children's Hospital, University Hospital Bonn, Bonn, Germany. Electronic address: Bernd.hoppe@knz-bonn.de.
Kidney Int ; 103(1): 207-217, 2023 01.
Article em En | MEDLINE | ID: mdl-36007597

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hiperoxalúria / Hiperoxalúria Primária Tipo de estudo: Clinical_trials / Prognostic_studies Limite: Humans Idioma: En Revista: Kidney Int Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hiperoxalúria / Hiperoxalúria Primária Tipo de estudo: Clinical_trials / Prognostic_studies Limite: Humans Idioma: En Revista: Kidney Int Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos