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Long-Term Immune Reconstitution in ADA-Deficient Patients Treated With Elapegademase: A Real-World Experience.
Murguia-Favela, Luis; Suresh, Sneha; Wright, Nicola A M; Alvi, Saima; Tehseen, Sarah; Hernandez-Trujillo, Vivian; Seroogy, Christine M; Haddad, Elie; Nieves, Daime; Hershfield, Michael S; Walter, Jolan E; Pettiford, Leah; Kamani, Naynesh R; Keller, Michael D; Pham-Huy, Anne; Grunebaum, Eyal.
Afiliação
  • Murguia-Favela L; Section of Hematology/Immunology, Department of Pediatrics, Alberta Children's Hospital and the University of Calgary, Calgary, Alberta, Canada.
  • Suresh S; Division of IHOPE, Department of Pediatrics, University of Alberta, Stollery Children's Hospital, Edmonton, Alberta, Canada.
  • Wright NAM; Section of Hematology/Immunology, Department of Pediatrics, Alberta Children's Hospital and the University of Calgary, Calgary, Alberta, Canada.
  • Alvi S; Division of Pediatric Hematology/Oncology, Jim Pattison Children's Hospital, Saskatoon, Saskatchewan, Canada.
  • Tehseen S; Division of Hematology/Oncology and Transfusion Medicine, Jim Pattison Children's Hospital, Saskatoon, Saskatchewan, Canada.
  • Hernandez-Trujillo V; Allergy and Immunology Care Center of South Florida, Miami Lakes, Fla.
  • Seroogy CM; Division of Allergy, Immunology & Rheumatology, University of Wisconsin School of Medicine and Public Health, Madison, Wis.
  • Haddad E; Division of Immunology and Rheumatology, Department of Pediatrics, Centre Hospitalier Universitaire (CHU) Sainte-Justine, University of Montreal, Montreal, Quebec, Canada.
  • Nieves D; Division of Pediatric Allergy and Immunology, University of South Florida at Johns Hopkins All Children's Hospital, St Petersburg, Fla.
  • Hershfield MS; Division of Medicine and Biochemistry, Duke University Medical Center, Durham, NC.
  • Walter JE; Division of Pediatric Allergy and Immunology, University of South Florida at Johns Hopkins All Children's Hospital, St Petersburg, Fla.
  • Pettiford L; Division of Allergy and Immunology, Children's National Hospital, Washington, DC.
  • Kamani NR; Division of Allergy and Immunology, Children's National Hospital, Washington, DC.
  • Keller MD; Division of Allergy and Immunology, Children's National Hospital, Washington, DC.
  • Pham-Huy A; Division of Infectious Diseases, Immunology and Allergy, Children's Hospital Eastern Ontario, Ottawa, Ontario, Canada.
  • Grunebaum E; Division of Immunology and Allergy, The Hospital for Sick Children, Toronto, Ontario, Canada. Electronic address: eyal.grunebaum@sickkids.ca.
J Allergy Clin Immunol Pract ; 11(6): 1725-1733, 2023 06.
Article em En | MEDLINE | ID: mdl-36736953

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Imunodeficiência Combinada Severa / Reconstituição Imune Limite: Animals / Humans / Infant Idioma: En Revista: J Allergy Clin Immunol Pract Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Canadá

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Imunodeficiência Combinada Severa / Reconstituição Imune Limite: Animals / Humans / Infant Idioma: En Revista: J Allergy Clin Immunol Pract Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Canadá