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Prime editing-mediated correction of the CFTR W1282X mutation in iPSCs and derived airway epithelial cells.
Li, Chao; Liu, Zhong; Anderson, Justin; Liu, Zhongyu; Tang, Liping; Li, Yao; Peng, Ning; Chen, Jianguo; Liu, Xueming; Fu, Lianwu; Townes, Tim M; Rowe, Steven M; Bedwell, David M; Guimbellot, Jennifer; Zhao, Rui.
Afiliação
  • Li C; Department of Biochemistry and Molecular Genetics, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Liu Z; Department of Biochemistry and Molecular Genetics, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Anderson J; Department of Pediatrics, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Liu Z; Gregory Fleming James Cystic Fibrosis Research Center, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Tang L; Gregory Fleming James Cystic Fibrosis Research Center, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Li Y; Gregory Fleming James Cystic Fibrosis Research Center, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Peng N; Department of Medicine, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Chen J; Gregory Fleming James Cystic Fibrosis Research Center, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Liu X; Department of Medicine, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Fu L; Gregory Fleming James Cystic Fibrosis Research Center, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Townes TM; Department of Medicine, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Rowe SM; Gregory Fleming James Cystic Fibrosis Research Center, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Bedwell DM; Department of Medicine, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
  • Guimbellot J; Key Laboratory of Imaging Processing and Intelligent Control, School of Artificial Intelligence and Automation, Huazhong University of Science and Technology, Wuhan, Hubei, China.
  • Zhao R; Department of Biochemistry and Molecular Genetics, School of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America.
PLoS One ; 18(11): e0295009, 2023.
Article em En | MEDLINE | ID: mdl-38019847

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Fibrose Cística / Células-Tronco Pluripotentes Induzidas Limite: Humans Idioma: En Revista: PLoS One Assunto da revista: CIENCIA / MEDICINA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Fibrose Cística / Células-Tronco Pluripotentes Induzidas Limite: Humans Idioma: En Revista: PLoS One Assunto da revista: CIENCIA / MEDICINA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos