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Membrane Stabilization by Modified Steroid Offers a Potential Therapy for Muscular Dystrophy Due to Dysferlin Deficit.
Sreetama, Sen Chandra; Chandra, Goutam; Van der Meulen, Jack H; Ahmad, Mohammad Mahad; Suzuki, Peter; Bhuvanendran, Shivaprasad; Nagaraju, Kanneboyina; Hoffman, Eric P; Jaiswal, Jyoti K.
Afiliación
  • Sreetama SC; Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC 20010, USA.
  • Chandra G; Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC 20010, USA.
  • Van der Meulen JH; Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC 20010, USA.
  • Ahmad MM; Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC 20010, USA.
  • Suzuki P; Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC 20010, USA.
  • Bhuvanendran S; Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC 20010, USA.
  • Nagaraju K; Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC 20010, USA; Department of Pharmaceutical Sciences, School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY 13902, USA.
  • Hoffman EP; Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC 20010, USA; Department of Pharmaceutical Sciences, School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY 13902, USA.
  • Jaiswal JK; Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC 20010, USA; Department of Genomics and Precision Medicine, George Washington University School of Medicine and Health Sciences, Washington, DC 20010, USA. Electronic address: jkjaiswal@cnmc.org.
Mol Ther ; 26(9): 2231-2242, 2018 09 05.
Article en En | MEDLINE | ID: mdl-30166241

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Esteroides / Disferlina / Distrofias Musculares Límite: Adolescent / Animals / Humans / Male Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2018 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Esteroides / Disferlina / Distrofias Musculares Límite: Adolescent / Animals / Humans / Male Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2018 Tipo del documento: Article País de afiliación: Estados Unidos