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Long-term safety and efficacy of selumetinib in children with neurofibromatosis type 1 on a phase 1/2 trial for inoperable plexiform neurofibromas.
Gross, Andrea M; Dombi, Eva; Wolters, Pamela L; Baldwin, Andrea; Dufek, Anne; Herrera, Kailey; Martin, Staci; Derdak, Joanne; Heisey, Kara S; Whitcomb, Patricia M; Steinberg, Seth M; Venzon, David J; Fisher, Michael J; Kim, AeRang; Bornhorst, Miriam; Weiss, Brian D; Blakeley, Jaishri O; Smith, Malcolm A; Widemann, Brigitte C.
Afiliación
  • Gross AM; Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland, USA.
  • Dombi E; Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland, USA.
  • Wolters PL; Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland, USA.
  • Baldwin A; Leidos, Clinical Research Directorate (CRD), Frederick National Laboratory for Cancer Research, Frederick, Maryland, USA.
  • Dufek A; Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland, USA.
  • Herrera K; Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland, USA.
  • Martin S; Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland, USA.
  • Derdak J; Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland, USA.
  • Heisey KS; Leidos, Clinical Research Directorate (CRD), Frederick National Laboratory for Cancer Research, Frederick, Maryland, USA.
  • Whitcomb PM; Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland, USA.
  • Steinberg SM; Biostatistics and Data Management Section, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland 20892, USA.
  • Venzon DJ; Biostatistics and Data Management Section, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland 20892, USA.
  • Fisher MJ; Children's Hospital of Philadelphia, Section of Neuro-Oncology, Philadelphia, Pennsylvania, USA.
  • Kim A; Children's National Hospital, Center for Cancer and Blood Disorders, Washington, District of Columbia, USA.
  • Bornhorst M; Children's National Hospital, Center for Cancer and Blood Disorders, Washington, District of Columbia, USA.
  • Weiss BD; Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, USA.
  • Blakeley JO; Johns Hopkins University, Division of Neurology, Baltimore, Maryland, USA.
  • Smith MA; Cancer Therapy Evaluation Program, National Cancer Institute, Bethesda, Maryland, USA.
  • Widemann BC; Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, Bethesda, Maryland, USA.
Neuro Oncol ; 25(10): 1883-1894, 2023 10 03.
Article en En | MEDLINE | ID: mdl-37115514

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Neurofibromatosis 1 / Neurofibroma Plexiforme Límite: Child / Humans Idioma: En Revista: Neuro Oncol Asunto de la revista: NEOPLASIAS / NEUROLOGIA Año: 2023 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Neurofibromatosis 1 / Neurofibroma Plexiforme Límite: Child / Humans Idioma: En Revista: Neuro Oncol Asunto de la revista: NEOPLASIAS / NEUROLOGIA Año: 2023 Tipo del documento: Article País de afiliación: Estados Unidos