Exon Skipping Therapy.

Young, Courtney S; Pyle, April D

Young, Courtney S; Pyle, April D.

Afiliação

Young CS; Molecular Biology Interdepartmental Program, Center for Duchenne Muscular Dystrophy, Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, University of California, Los Angeles, Los Angeles, CA 90095.
Pyle AD; Molecular Biology Interdepartmental Program, Center for Duchenne Muscular Dystrophy, Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, University of California, Los Angeles, Los Angeles, CA 90095; Department of Microbiology, Immunology and Molecular Genetics, University of California, Los Angeles, Los Angeles, CA 90095. Electronic address: apyle@mednet.ucla.edu.

Cell ; 167(5): 1144, 2016 Nov 17.

Article em En | MEDLINE | ID: mdl-27863231

Assuntos

Distrofina/genética; Terapia Genética; Distrofia Muscular de Duchenne/genética; Distrofia Muscular de Duchenne/terapia; Éxons; Humanos; Fases de Leitura; Estados Unidos; United States Food and Drug Administration

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Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Distrofina / Distrofia Muscular de Duchenne Limite: Humans País/Região como assunto: America do norte Idioma: En Revista: Cell Ano de publicação: 2016 Tipo de documento: Article

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