Your browser doesn't support javascript.
loading
Long-term comparative effectiveness of pegvaliase versus standard of care comparators in adults with phenylketonuria.
Zori, Roberto; Ahring, Kirsten; Burton, Barbara; Pastores, Gregory M; Rutsch, Frank; Jha, Ashok; Jurecki, Elaina; Rowell, Richard; Harding, Cary.
Afiliação
  • Zori R; University of Florida Health, Gainesville, FL, USA. Electronic address: zorirt@peds.ufl.edu.
  • Ahring K; Copenhagen University Hospital, Department of Paediatrics, PKU Clinic, Copenhagen, Denmark. Electronic address: kirsten.kiaer.ahring@regionh.dk.
  • Burton B; Lurie Children's Hospital, Chicago, IL, USA. Electronic address: bburton@luriechildrens.org.
  • Pastores GM; Mater Misericordiae University Hospital, University College Dublin, Dublin, Ireland. Electronic address: gpastores@mater.ie.
  • Rutsch F; Münster University Children's Hospital, Department of General Pediatrics, Münster, Germany. Electronic address: rutschf@ukmuenster.de.
  • Jha A; BioMarin Europe Ltd., London, UK. Electronic address: ashok.jha@bmrn.com.
  • Jurecki E; BioMarin Pharmaceutical Inc., Novato, CA, USA. Electronic address: EJurecki@bmrn.com.
  • Rowell R; BioMarin Pharmaceutical Inc., Novato, CA, USA. Electronic address: richard.rowell@bmrn.com.
  • Harding C; Oregon Health & Science University, Portland, OR, USA. Electronic address: hardingc@ohsu.edu.
Mol Genet Metab ; 128(1-2): 92-101, 2019.
Article em En | MEDLINE | ID: mdl-31439512

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Fenilalanina Amônia-Liase / Fenilcetonúrias / Proteínas Recombinantes / Padrão de Cuidado Tipo de estudo: Prognostic_studies Limite: Adolescent / Adult / Female / Humans / Male / Middle aged Idioma: En Revista: Mol Genet Metab Assunto da revista: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Fenilalanina Amônia-Liase / Fenilcetonúrias / Proteínas Recombinantes / Padrão de Cuidado Tipo de estudo: Prognostic_studies Limite: Adolescent / Adult / Female / Humans / Male / Middle aged Idioma: En Revista: Mol Genet Metab Assunto da revista: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Ano de publicação: 2019 Tipo de documento: Article