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Deciphering the Ets-1/2-mediated transcriptional regulation of F8 gene identifies a minimal F8 promoter for hemophilia A gene therapy.
Famà, Rosella; Borroni, Ester; Merlin, Simone; Airoldi, Chiara; Pignani, Silvia; Cucci, Alessia; Corà, Davide; Bruscaggin, Valentina; Scardellato, Sharon; Faletti, Stefania; Pelicci, Giuliana; Pinotti, Mirko; Walker, Gillian E; Follenzi, Antonia.
Afiliação
  • Famà R; Department of Health Sciences, Università del Piemonte Orientale, Novara, Italy.
  • Borroni E; Department of Health Sciences, Università del Piemonte Orientale, Novara, Italy.
  • Merlin S; Department of Health Sciences, Università del Piemonte Orientale, Novara, Italy.
  • Airoldi C; Department of Translational Medicine, Università del Piemonte Orientale, Novara, Italy.
  • Pignani S; Department of Health Sciences, Università del Piemonte Orientale, Novara, Italy.
  • Cucci A; Department of Health Sciences, Università del Piemonte Orientale, Novara, Italy.
  • Corà D; Department of Translational Medicine, Center for Translational Research on Autoimmune and Allergic Disease (CAAD), University of Piemonte Orientale, Novara, Italy.
  • Bruscaggin V; Department of Health Sciences, Università del Piemonte Orientale, Novara, Italy.
  • Scardellato S; Department of Health Sciences, Università del Piemonte Orientale, Novara, Italy.
  • Faletti S; Department of Experimental Oncology, IEO, European Institute of Oncology IRCCS, Milan, Italy.
  • Pelicci G; Department of Health Sciences, Università del Piemonte Orientale, Novara, Italy.
  • Pinotti M; Department of Life Sciences and Biotechnology, Universita' di Ferrara, Italy.
  • Walker GE; Department of Health Sciences, Università del Piemonte Orientale, Novara, Italy.
  • Follenzi A; Department of Health Sciences, Università del Piemonte Orientale, Novara, Italy.
Haematologica ; 106(6): 1624-1635, 2021 06 01.
Article em En | MEDLINE | ID: mdl-32467137

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Fator VIII / Hemofilia A Tipo de estudo: Prognostic_studies Limite: Animals Idioma: En Revista: Haematologica Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Itália

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Fator VIII / Hemofilia A Tipo de estudo: Prognostic_studies Limite: Animals Idioma: En Revista: Haematologica Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Itália