Your browser doesn't support javascript.
loading
Combination of lentiviral and genome editing technologies for the treatment of sickle cell disease.
Ramadier, Sophie; Chalumeau, Anne; Felix, Tristan; Othman, Nadia; Aknoun, Sherazade; Casini, Antonio; Maule, Giulia; Masson, Cecile; De Cian, Anne; Frati, Giacomo; Brusson, Megane; Concordet, Jean-Paul; Cavazzana, Marina; Cereseto, Anna; El Nemer, Wassim; Amendola, Mario; Wattellier, Benoit; Meneghini, Vasco; Miccio, Annarita.
Afiliação
  • Ramadier S; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM UMR1163, 75015 Paris, France; Université de Paris, 75015 Paris, France; Phasics, Bâtiment Explorer, Espace Technologique, Route de l'Orme des Merisiers, 91190 St. Aubin, France.
  • Chalumeau A; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM UMR1163, 75015 Paris, France; Université de Paris, 75015 Paris, France.
  • Felix T; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM UMR1163, 75015 Paris, France; Université de Paris, 75015 Paris, France.
  • Othman N; Phasics, Bâtiment Explorer, Espace Technologique, Route de l'Orme des Merisiers, 91190 St. Aubin, France.
  • Aknoun S; Phasics, Bâtiment Explorer, Espace Technologique, Route de l'Orme des Merisiers, 91190 St. Aubin, France.
  • Casini A; CIBIO, University of Trento, 38100 Trento, Italy.
  • Maule G; CIBIO, University of Trento, 38100 Trento, Italy.
  • Masson C; Paris-Descartes Bioinformatics Platform, Imagine Institute, 75015 Paris, France.
  • De Cian A; INSERM U1154, CNRS UMR7196, Museum National d'Histoire Naturelle, 75015 Paris, France.
  • Frati G; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM UMR1163, 75015 Paris, France; Université de Paris, 75015 Paris, France.
  • Brusson M; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM UMR1163, 75015 Paris, France; Université de Paris, 75015 Paris, France.
  • Concordet JP; INSERM U1154, CNRS UMR7196, Museum National d'Histoire Naturelle, 75015 Paris, France.
  • Cavazzana M; Université de Paris, 75015 Paris, France; Imagine Institute, 75015 Paris, France; Biotherapy Department and Clinical Investigation Center, Assistance Publique Hôpitaux de Paris, INSERM, 75015 Paris, France.
  • Cereseto A; CIBIO, University of Trento, 38100 Trento, Italy.
  • El Nemer W; Etablissement Français du Sang PACA-Corse, Marseille, France; Aix Marseille Université, EFS, CNRS, ADES, "Biologie des Groupes Sanguins," 13000 Marseille, France; Laboratoire d'Excellence GR-Ex, Paris, France.
  • Amendola M; Genethon, INSERM UMR951, 91000 Evry, France.
  • Wattellier B; Phasics, Bâtiment Explorer, Espace Technologique, Route de l'Orme des Merisiers, 91190 St. Aubin, France.
  • Meneghini V; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM UMR1163, 75015 Paris, France; Université de Paris, 75015 Paris, France. Electronic address: meneghini.vasco@hsr.it.
  • Miccio A; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM UMR1163, 75015 Paris, France; Université de Paris, 75015 Paris, France. Electronic address: annarita.miccio@institutimagine.org.
Mol Ther ; 30(1): 145-163, 2022 01 05.
Article em En | MEDLINE | ID: mdl-34418541

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Edição de Genes / Anemia Falciforme Limite: Humans Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: França

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Edição de Genes / Anemia Falciforme Limite: Humans Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: França