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Delivery of AAV-based gene therapy through haemophilia centres-A need for re-evaluation of infrastructure and comprehensive care: A Joint publication of EAHAD and EHC.
Miesbach, Wolfgang; Chowdary, Pratima; Coppens, Michiel; Hart, Daniel P; Jimenez-Yuste, Victor; Klamroth, Robert; Makris, Michael; Noone, Declan; Peyvandi, Flora.
Afiliação
  • Miesbach W; Medical Clinic 2, Institute of Transfusion Medicine, University Hospital Frankfurt, Frankfurt, Germany.
  • Chowdary P; Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, UK.
  • Coppens M; Department of Vascular Medicine, Haemophilia Treatment Centre, Amsterdam Cardiovascular Sciences, Amsterdam University Medical Centres, University of Amsterdam, Amsterdam, The Netherlands.
  • Hart DP; The Royal London Hospital Haemophilia Centre, Barts and The London School of Medicine and Dentistry, QMUL, London, UK.
  • Jimenez-Yuste V; Hematology Department, Hospital Universitario La Paz, Autonoma University, Madrid, Spain.
  • Klamroth R; Department for Internal Medicine and Vascular Medicine, Haemophilia Treatment Centre, Vivantes Hospital im Friedrichshain, Berlin, Germany.
  • Makris M; Department of Infection, Immunity and Cardiovascular Disease, University of Sheffield, Sheffield, UK.
  • Noone D; European Haemophilia Consortium, Brussels, Belgium.
  • Peyvandi F; Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Haemophilia and Thrombosis Centre and Fondazione Luigi Villa, Milan, Italy.
Haemophilia ; 27(6): 967-973, 2021 Nov.
Article em En | MEDLINE | ID: mdl-34553460

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Dependovirus / Hemofilia A Tipo de estudo: Prognostic_studies Limite: Humans Idioma: En Revista: Haemophilia Assunto da revista: HEMATOLOGIA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Alemanha

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Dependovirus / Hemofilia A Tipo de estudo: Prognostic_studies Limite: Humans Idioma: En Revista: Haemophilia Assunto da revista: HEMATOLOGIA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Alemanha