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Patisiran treatment in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy after liver transplantation.
Schmidt, Hartmut H; Wixner, Jonas; Planté-Bordeneuve, Violaine; Muñoz-Beamud, Francisco; Lladó, Laura; Gillmore, Julian D; Mazzeo, Anna; Li, Xingyu; Arum, Seth; Jay, Patrick Y; Adams, David.
Afiliação
  • Schmidt HH; Department of Gastroenterology, Hepatology and Transplant Medicine, University Hospital Essen, University of Duisburg-Essen (formerly of University Hospital Munster, Munster, Germany), Essen, Germany.
  • Wixner J; Department of Public Health and Clinical Medicine, Umeå University, Umeå, Sweden.
  • Planté-Bordeneuve V; Department of Neurology, East Paris University, Hospital Henri Mondor - Public Assistance Hospital of Paris, Créteil, France.
  • Muñoz-Beamud F; Mondor Biomedical Research Institute - IMRB, INSERM, U955 Team 10 "Biology of the Neuro-Muscular System", Créteil, France.
  • Lladó L; Hereditary Amyloidosis Unit, Department of Internal Medicine, Juan Ramón Jiménez Hospital, Huelva, Spain.
  • Gillmore JD; Liver Transplantation Unit, Department of Surgery, and the Multidisciplinary Familial Amyloidosis Unit, Hospital Universitari de Bellvitge, Barcelona, Spain.
  • Mazzeo A; Biomedical Research Institute, IDIBELL, University of Barcelona, Barcelona, Spain.
  • Li X; National Amyloidosis Centre, Division of Medicine, University College London Medical School, London, UK.
  • Arum S; Unit of Neurology and Neuromuscular Diseases, Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.
  • Jay PY; Alnylam Pharmaceuticals, Inc, Cambridge, Massachusetts, USA.
  • Adams D; Alnylam Pharmaceuticals, Inc, Cambridge, Massachusetts, USA.
Am J Transplant ; 22(6): 1646-1657, 2022 06.
Article em En | MEDLINE | ID: mdl-35213769

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Polineuropatias / Transplante de Fígado / Neuropatias Amiloides Familiares Tipo de estudo: Etiology_studies Limite: Humans Idioma: En Revista: Am J Transplant Assunto da revista: TRANSPLANTE Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Alemanha

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Polineuropatias / Transplante de Fígado / Neuropatias Amiloides Familiares Tipo de estudo: Etiology_studies Limite: Humans Idioma: En Revista: Am J Transplant Assunto da revista: TRANSPLANTE Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Alemanha