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Nusinersen Induces Disease-Severity-Specific Neurometabolic Effects in Spinal Muscular Atrophy.
Errico, Francesco; Marino, Carmen; Grimaldi, Manuela; Nuzzo, Tommaso; Bassareo, Valentina; Valsecchi, Valeria; Panicucci, Chiara; Di Schiavi, Elia; Mazza, Tommaso; Bruno, Claudio; D'Amico, Adele; Carta, Manolo; D'Ursi, Anna Maria; Bertini, Enrico; Pellizzoni, Livio; Usiello, Alessandro.
Afiliação
  • Errico F; Laboratory of Translational Neuroscience, Ceinge Biotecnologie Avanzate, 80145 Naples, Italy.
  • Marino C; Department of Agricultural Sciences, University of Naples "Federico II", 80055 Portici, Italy.
  • Grimaldi M; Department of Pharmacy, University of Salerno, 84084 Fisciano, Italy.
  • Nuzzo T; Department of Pharmacy, University of Salerno, 84084 Fisciano, Italy.
  • Bassareo V; Laboratory of Translational Neuroscience, Ceinge Biotecnologie Avanzate, 80145 Naples, Italy.
  • Valsecchi V; Department of Environmental, Biological and Pharmaceutical Science and Technologies, Università degli Studi della Campania "Luigi Vanvitelli", 81100 Caserta, Italy.
  • Panicucci C; Department of Biomedical Sciences, University of Cagliari, 09042 Monserrato, Italy.
  • Di Schiavi E; Division of Pharmacology, Department of Neuroscience, Reproductive and Dentistry Sciences, School of Medicine, University of Naples "Federico II", 80131 Naples, Italy.
  • Mazza T; Center of Translational and Experimental Myology, IRCCS Istituto Giannina Gaslini, 16147 Genoa, Italy.
  • Bruno C; Institute of Biosciences and BioResources (IBBR), CNR, 80131 Naples, Italy.
  • D'Amico A; IRCCS Casa Sollievo della Sofferenza, Bioinformatics Unit, 71013 San Giovanni Rotondo, Italy.
  • Carta M; Center of Translational and Experimental Myology, IRCCS Istituto Giannina Gaslini, 16147 Genoa, Italy.
  • D'Ursi AM; Department of Neuroscience, Rehabilitation, Ophtalmology, Genetics, Maternal and Child Health-DINOGMI, University of Genova, 16132 Genoa, Italy.
  • Bertini E; Unit of Neuromuscular and Neurodegenerative Disorders, Department of Neurosciences, Bambino Gesù Children's Hospital IRCCS, 00163 Roma, Italy.
  • Pellizzoni L; Department of Biomedical Sciences, University of Cagliari, 09042 Monserrato, Italy.
  • Usiello A; Department of Pharmacy, University of Salerno, 84084 Fisciano, Italy.
Biomolecules ; 12(10)2022 10 06.
Article em En | MEDLINE | ID: mdl-36291640

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal Limite: Humans Idioma: En Revista: Biomolecules Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Itália

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal Limite: Humans Idioma: En Revista: Biomolecules Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Itália