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Long-term efficacy of nusinersen and its evaluation in adolescent and adult patients with spinal muscular atrophy types 1 and 2.
Iwayama, Hideyuki; Kawahara, Kohei; Takagi, Mizuki; Numoto, Shingo; Azuma, Yoshiteru; Kurahashi, Hirokazu; Yasue, Yumiko; Kawajiri, Hiroyuki; Yanase, Atsushi; Ito, Teruyoshi; Kimura, Shinya; Kumagai, Toshiyuki; Okumura, Akihisa.
Afiliação
  • Iwayama H; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan. Electronic address: iwahide1976@gmail.com.
  • Kawahara K; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.
  • Takagi M; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.
  • Numoto S; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.
  • Azuma Y; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.
  • Kurahashi H; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.
  • Yasue Y; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.
  • Kawajiri H; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.
  • Yanase A; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.
  • Ito T; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.
  • Kimura S; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.
  • Kumagai T; Department of Pediatric Neurology, Aichi Prefectural Colony Central Hospital, Kasugai, Japan; Kuma Home Medical Care Clinic, Nagoya, Japan.
  • Okumura A; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.
Brain Dev ; 45(2): 110-116, 2023 Feb.
Article em En | MEDLINE | ID: mdl-36335004

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância / COVID-19 Limite: Adolescent / Adult / Child / Child, preschool / Humans / Infant Idioma: En Revista: Brain Dev Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância / COVID-19 Limite: Adolescent / Adult / Child / Child, preschool / Humans / Infant Idioma: En Revista: Brain Dev Ano de publicação: 2023 Tipo de documento: Article