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Human heterologous liver cells transiently improve hyperammonemia and ureagenesis in individuals with severe urea cycle disorders.
Meyburg, Jochen; Opladen, Thomas; Spiekerkötter, Ute; Schlune, Andrea; Schenk, Jens-Peter; Schmidt, Jan; Weitz, Jürgen; Okun, Jürgen; Bürger, Friederike; Omran, Tawfeg Ben; Abdoh, Ghassan; Al Rifai, Hilal; Monavari, Ahmad; Konstantopoulou, Vassiliki; Kölker, Stefan; Yudkoff, Marc; Hoffmann, Georg F.
Afiliação
  • Meyburg J; Centre for Child and Adolescent Medicine, University Hospital Heidelberg, Im Neuenheimer Feld 430, D-69120, Heidelberg, Germany. jochen.meyburg@med.uni-heidelberg.de.
  • Opladen T; Centre for Child and Adolescent Medicine, University Hospital Heidelberg, Im Neuenheimer Feld 430, D-69120, Heidelberg, Germany.
  • Spiekerkötter U; Department of General Pediatrics, Neonatology and Paediatric Cardiology, Medical Faculty, Heinrich-Heine-University, Duesseldorf, Germany.
  • Schlune A; Division of General Pediatrics, University Children's Hospital, Freiburg, Germany.
  • Schenk JP; Department of General Pediatrics, Neonatology and Paediatric Cardiology, Medical Faculty, Heinrich-Heine-University, Duesseldorf, Germany.
  • Schmidt J; Division of Pediatric Radiology, Department of Diagnostic and Interventional Radiology, University Hospital, Heidelberg, Germany.
  • Weitz J; Department of Visceral and Transplant Surgery, University Hospital, Heidelberg, Germany.
  • Okun J; Department of Visceral and Transplant Surgery, University Hospital, Heidelberg, Germany.
  • Bürger F; Centre for Child and Adolescent Medicine, University Hospital Heidelberg, Im Neuenheimer Feld 430, D-69120, Heidelberg, Germany.
  • Omran TB; Centre for Child and Adolescent Medicine, University Hospital Heidelberg, Im Neuenheimer Feld 430, D-69120, Heidelberg, Germany.
  • Abdoh G; Department of Pediatrics, Hamad Medical Corporation, Doha, Qatar.
  • Al Rifai H; Department of Pediatrics, Hamad Medical Corporation, Doha, Qatar.
  • Monavari A; Department of Pediatrics, Hamad Medical Corporation, Doha, Qatar.
  • Konstantopoulou V; National Centre of Inherited Metabolic Disorders, Dublin, Ireland.
  • Kölker S; Division of Pulmonology, Allergology, Endocrinology, and Metabolic Medicine, University Children's Hospital, Vienna, Austria.
  • Yudkoff M; Centre for Child and Adolescent Medicine, University Hospital Heidelberg, Im Neuenheimer Feld 430, D-69120, Heidelberg, Germany.
  • Hoffmann GF; Division of Metabolic Diseases, Children's Hospital of Philadelphia, Philadelphia, USA.
J Inherit Metab Dis ; 41(1): 81-90, 2018 01.
Article em En | MEDLINE | ID: mdl-29027067

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Ureia / Transplante de Fígado / Transplante de Células / Hiperamonemia / Distúrbios Congênitos do Ciclo da Ureia / Amônia / Fígado Tipo de estudo: Clinical_trials / Diagnostic_studies / Etiology_studies / Guideline / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Female / Humans / Infant / Male / Newborn País/Região como assunto: Europa Idioma: En Revista: J Inherit Metab Dis Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Alemanha

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Ureia / Transplante de Fígado / Transplante de Células / Hiperamonemia / Distúrbios Congênitos do Ciclo da Ureia / Amônia / Fígado Tipo de estudo: Clinical_trials / Diagnostic_studies / Etiology_studies / Guideline / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Female / Humans / Infant / Male / Newborn País/Região como assunto: Europa Idioma: En Revista: J Inherit Metab Dis Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Alemanha