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Sotatercept, a novel transforming growth factor ß ligand trap, improves anemia in ß-thalassemia: a phase II, open-label, dose-finding study.
Cappellini, Maria Domenica; Porter, John; Origa, Raffaella; Forni, Gian Luca; Voskaridou, Ersi; Galactéros, Frédéric; Taher, Ali T; Arlet, Jean-Benoît; Ribeil, Jean-Antoine; Garbowski, Maciej; Graziadei, Giovanna; Brouzes, Chantal; Semeraro, Michaela; Laadem, Abderrahmane; Miteva, Dimana; Zou, Jun; Sung, Victoria; Zinger, Tatiana; Attie, Kenneth M; Hermine, Olivier.
Afiliação
  • Cappellini MD; Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Department of Clinical Sciences and Community Health, University of Milan, Italy maria.cappellini@unimi.it olivier.hermine@nck.aphp.fr.
  • Porter J; Department of Haematology, University College London, UK.
  • Origa R; Day Hospital Talassemia, Ospedale Pediatrico Microcitemico "A. Cao", A.O. "G. Brotzu", Cagliari, Italy.
  • Forni GL; Centro della Microcitemia, Ospedali Galliera, Genova, Italy.
  • Voskaridou E; Thalassemia Center, Laikon General Hospital, Athens, Greece.
  • Galactéros F; UMGGR, Hôpital Henri Mondor; Assistance Publique-Hôpitaux de Paris (APHP); UPEC, Créteil, France.
  • Taher AT; Department of Internal Medicine, American University of Beirut Medical Center, Lebanon.
  • Arlet JB; Department of Internal Medicine, APHP, Hôpital Européen Georges-Pompidou, Paris, France.
  • Ribeil JA; INSERM UMR1163, CNRS ERL 8254, Institut Imagine, Université Paris Descartes-Sorbonne Paris Cité, France.
  • Garbowski M; Laboratory of Excellence GR-Ex, Paris, France.
  • Graziadei G; Laboratory of Onco-hematology, Hôpital Necker-Enfants Malades, Paris, France.
  • Brouzes C; Department of Haematology, University College London, UK.
  • Semeraro M; Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Department of Clinical Sciences and Community Health, University of Milan, Italy.
  • Laadem A; Laboratory of Onco-hematology, Hôpital Necker-Enfants Malades, Paris, France.
  • Miteva D; Laboratory of Onco-hematology, Hôpital Necker-Enfants Malades, Paris, France.
  • Zou J; Celgene Corporation, Summit, NJ, USA.
  • Sung V; Celgene Corporation, Boudry, Switzerland.
  • Zinger T; Celgene Corporation, Summit, NJ, USA.
  • Attie KM; Celgene Corporation, San Francisco, CA, USA.
  • Hermine O; Celgene Corporation, Boudry, Switzerland.
Haematologica ; 104(3): 477-484, 2019 03.
Article em En | MEDLINE | ID: mdl-30337358

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Proteínas Recombinantes de Fusão / Talassemia beta / Anemia Tipo de estudo: Clinical_trials / Diagnostic_studies Limite: Adult / Female / Humans / Male / Middle aged Idioma: En Revista: Haematologica Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Proteínas Recombinantes de Fusão / Talassemia beta / Anemia Tipo de estudo: Clinical_trials / Diagnostic_studies Limite: Adult / Female / Humans / Male / Middle aged Idioma: En Revista: Haematologica Ano de publicação: 2019 Tipo de documento: Article