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Hematopoietic Stem Cell Transplantation as Treatment for Patients with DOCK8 Deficiency.
Aydin, Susanne E; Freeman, Alexandra F; Al-Herz, Waleed; Al-Mousa, Hamoud A; Arnaout, Rand K; Aydin, Roland C; Barlogis, Vincent; Belohradsky, Bernd H; Bonfim, Carmem; Bredius, Robbert G; Chu, Julia I; Ciocarlie, Oana C; Dogu, Figen; Gaspar, Hubert B; Geha, Raif S; Gennery, Andrew R; Hauck, Fabian; Hawwari, Abbas; Hickstein, Dennis D; Hoenig, Manfred; Ikinciogullari, Aydan; Klein, Christoph; Kumar, Ashish; Ifversen, Marianne R S; Matthes, Susanne; Metin, Ayse; Neven, Benedicte; Pai, Sung-Yun; Parikh, Suhag H; Picard, Capucine; Renner, Ellen D; Sanal, Özden; Schulz, Ansgar S; Schuster, Friedhelm; Shah, Nirali N; Shereck, Evan B; Slatter, Mary A; Su, Helen C; van Montfrans, Joris; Woessmann, Wilhelm; Ziegler, John B; Albert, Michael H.
Afiliação
  • Aydin SE; Dr von Hauner University Children's Hospital, Ludwig Maximilians Universität, Munich, Germany.
  • Freeman AF; National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, Md.
  • Al-Herz W; Department of Pediatrics, Al-Sabah Hospital, Kuwait, Kuwait.
  • Al-Mousa HA; Department of Pediatrics, King Faisal Specialist Hospital & Research Center, Riyadh, Saudi Arabia.
  • Arnaout RK; Department of Medicine, Allergy & Immunology, King Faisal Specialist Hospital & Research Center, Riyadh, Saudi Arabia.
  • Aydin RC; Dr von Hauner University Children's Hospital, Ludwig Maximilians Universität, Munich, Germany.
  • Barlogis V; Pediatric Hematology, Assistance publique des Hopitaux de Marseille, Marseille, France.
  • Belohradsky BH; Deutsche Selbsthilfe Angeborene Immundefekte, Schnaitsee, Germany.
  • Bonfim C; Pediatric Blood and Marrow Transplantation Program, Hospital de Clinicas, Federal University of Parana, Curitiba, Brazil.
  • Bredius RG; Pediatric Immunology, LUMC, Leiden, The Netherlands.
  • Chu JI; Department of Pediatrics, Stanford University School of Medicine, Stanford, Calif.
  • Ciocarlie OC; Department of Bone Marrow Transplantation, Great Ormond Street Hospital NHS Trust, London, United Kingdom.
  • Dogu F; Department of Pediatric Immunology & Allergy, Ankara University School of Medicine, Ankara, Turkey.
  • Gaspar HB; Molecular Immunology Unit, UCL Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Geha RS; Department of Immunology, Boston Children's Hospital, Boston, Mass.
  • Gennery AR; Institute of Cellular Medicine, Newcastle University, Newcastle upon Tyne, United Kingdom.
  • Hauck F; Dr von Hauner University Children's Hospital, Ludwig Maximilians Universität, Munich, Germany.
  • Hawwari A; King Abdullah International Medical Research Center, Riyadh, Saudi Arabia.
  • Hickstein DD; ETI/CCR/NCI, National Institutes of Health, Bethesda, Md.
  • Hoenig M; Department of Pediatrics, University Medical Center Ulm, Ulm, Germany.
  • Ikinciogullari A; Department of Pediatric Immunology & Allergy, Ankara University School of Medicine, Ankara, Turkey.
  • Klein C; Dr von Hauner University Children's Hospital, Ludwig Maximilians Universität, Munich, Germany.
  • Kumar A; BMT/Immune Deficiency, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio.
  • Ifversen MRS; Department for Children and Adolescents, Rigshospitalet, University of Copenhagen, Copenhagen, Denmark.
  • Matthes S; Stem Cell Transplantation, St Anna Children's Hospital, Vienna, Austria.
  • Metin A; Pediatric Immunology, Ankara Children's Hematology Oncology Training and Research Hospital, Ankara, Turkey.
  • Neven B; Department for Pediatric Immuno-Hematology and Rheumatology, Necker Hospital, Paris, France.
  • Pai SY; Boston Children's Hospital, Dana-Farber Cancer Institute, Boston, Mass.
  • Parikh SH; Pediatric Blood and Marrow Transplant Program, Duke University Medical Center, Durham, NC.
  • Picard C; Study Center of Primary Immunodeficiency, Necker Children's Hospital, Paris, France.
  • Renner ED; Environmental Medicine, TU Munich, Neuherberg, Germany.
  • Sanal Ö; Department of Pediatrics, Hacettepe University, Ankara, Turkey.
  • Schulz AS; Department of Pediatrics, University Medical Center Ulm, Ulm, Germany.
  • Schuster F; Department of Pediatrics, Düsseldorf University Hospital, Düsseldorf, Germany.
  • Shah NN; Pediatric Oncology Branch, National Cancer Institute, Bethesda, Md.
  • Shereck EB; Pediatric Hematology/Oncology, Oregon & Health Science University, Portland, Ore.
  • Slatter MA; Paediatric BMT, Great North Children's Hospital, Newcastle upon Tyne, United Kingdom.
  • Su HC; Laboratory of Clinical Immunology and Microbiology, NIAID, National Institutes of Health, Bethesda, Md.
  • van Montfrans J; Pediatric Immunology and Infectious Diseases, UMC Utrecht, Utrecht, The Netherlands.
  • Woessmann W; Department of Pediatric Hematology and Oncology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Ziegler JB; Immunology & Infectious Diseases, Sydney Children's Hospital, Randwick, NSW, Australia.
  • Albert MH; Dr von Hauner University Children's Hospital, Ludwig Maximilians Universität, Munich, Germany. Electronic address: malbert@med.lmu.de.
J Allergy Clin Immunol Pract ; 7(3): 848-855, 2019 03.
Article em En | MEDLINE | ID: mdl-30391550

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Transplante de Células-Tronco Hematopoéticas / Fatores de Troca do Nucleotídeo Guanina / Síndromes de Imunodeficiência Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male Idioma: En Revista: J Allergy Clin Immunol Pract Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Alemanha

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Transplante de Células-Tronco Hematopoéticas / Fatores de Troca do Nucleotídeo Guanina / Síndromes de Imunodeficiência Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male Idioma: En Revista: J Allergy Clin Immunol Pract Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Alemanha