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Comprehensive behavioral and biochemical outcomes of novel murine models of GM1-gangliosidosis and Morquio syndrome type B.
Przybilla, Michael J; Ou, Li; Tabaran, Alexandru-Flaviu; Jiang, Xuntian; Sidhu, Rohini; Kell, Pamela J; Ory, Daniel S; O'Sullivan, M Gerard; Whitley, Chester B.
Afiliação
  • Przybilla MJ; Gene Therapy Center, Department of Pediatrics, University of Minnesota, Minneapolis, MN, United States; Molecular, Cellular, Developmental Biology, and Genetics Graduate Program, University of Minnesota, Minneapolis, MN, United States.
  • Ou L; Gene Therapy Center, Department of Pediatrics, University of Minnesota, Minneapolis, MN, United States.
  • Tabaran AF; Comparative Pathology Shared Resource, Masonic Cancer Center and College of Veterinary Medicine, University of Minnesota, Saint Paul, MN, United States.
  • Jiang X; Department of Medicine, Washington University School of Medicine, Saint Louis, MO, United States.
  • Sidhu R; Department of Medicine, Washington University School of Medicine, Saint Louis, MO, United States.
  • Kell PJ; Department of Medicine, Washington University School of Medicine, Saint Louis, MO, United States.
  • Ory DS; Department of Medicine, Washington University School of Medicine, Saint Louis, MO, United States.
  • O'Sullivan MG; Comparative Pathology Shared Resource, Masonic Cancer Center and College of Veterinary Medicine, University of Minnesota, Saint Paul, MN, United States.
  • Whitley CB; Gene Therapy Center, Department of Pediatrics, University of Minnesota, Minneapolis, MN, United States; Molecular, Cellular, Developmental Biology, and Genetics Graduate Program, University of Minnesota, Minneapolis, MN, United States. Electronic address: whitley@umn.edu.
Mol Genet Metab ; 126(2): 139-150, 2019 02.
Article em En | MEDLINE | ID: mdl-30528226

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Gangliosidose GM1 / Beta-Galactosidase / Mucopolissacaridose IV / Modelos Animais de Doenças Limite: Animals Idioma: En Revista: Mol Genet Metab Assunto da revista: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Gangliosidose GM1 / Beta-Galactosidase / Mucopolissacaridose IV / Modelos Animais de Doenças Limite: Animals Idioma: En Revista: Mol Genet Metab Assunto da revista: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Estados Unidos