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Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome.
Collaud, Fanny; Bortolussi, Giulia; Guianvarc'h, Laurence; Aronson, Sem J; Bordet, Thierry; Veron, Philippe; Charles, Severine; Vidal, Patrice; Sola, Marcelo Simon; Rundwasser, Stephanie; Dufour, Delphine G; Lacoste, Florence; Luc, Cyril; Wittenberghe, Laetitia V; Martin, Samia; Le Bec, Christine; Bosma, Piter J; Muro, Andres F; Ronzitti, Giuseppe; Hebben, Matthias; Mingozzi, Federico.
Afiliação
  • Collaud F; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Bortolussi G; International Center for Genetic Engineering and Biotechnology, 34149 Trieste, Italy.
  • Guianvarc'h L; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Aronson SJ; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, 1105 BK Amsterdam, the Netherlands.
  • Bordet T; AFM-Telethon, 91000 Evry, France.
  • Veron P; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Charles S; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Vidal P; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Sola MS; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Rundwasser S; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Dufour DG; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Lacoste F; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Luc C; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Wittenberghe LV; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Martin S; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Le Bec C; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Bosma PJ; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, 1105 BK Amsterdam, the Netherlands.
  • Muro AF; International Center for Genetic Engineering and Biotechnology, 34149 Trieste, Italy.
  • Ronzitti G; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Hebben M; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
  • Mingozzi F; INTEGRARE, Genethon, INSERM, Univ. Evry, Université Paris-Saclay, 91002 Evry, France.
Mol Ther Methods Clin Dev ; 12: 157-174, 2019 Mar 15.
Article em En | MEDLINE | ID: mdl-30705921

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Prognostic_studies Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2019 Tipo de documento: Article País de afiliação: França

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Prognostic_studies Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2019 Tipo de documento: Article País de afiliação: França