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Nusinersen safety and effects on motor function in adult spinal muscular atrophy type 2 and 3.
Maggi, Lorenzo; Bello, Luca; Bonanno, Silvia; Govoni, Alessandra; Caponnetto, Claudia; Passamano, Luigia; Grandis, Marina; Trojsi, Francesca; Cerri, Federica; Ferraro, Manfredi; Bozzoni, Virginia; Caumo, Luca; Piras, Rachele; Tanel, Raffaella; Saccani, Elena; Meneri, Megi; Vacchiano, Veria; Ricci, Giulia; Soraru', Gianni; D'Errico, Eustachio; Tramacere, Irene; Bortolani, Sara; Pavesi, Giovanni; Zanin, Riccardo; Silvestrini, Mauro; Politano, Luisa; Schenone, Angelo; Previtali, Stefano Carlo; Berardinelli, Angela; Turri, Mara; Verriello, Lorenzo; Coccia, Michela; Mantegazza, Renato; Liguori, Rocco; Filosto, Massimiliano; Marrosu, Gianni; Siciliano, Gabriele; Simone, Isabella Laura; Mongini, Tiziana; Comi, Giacomo; Pegoraro, Elena.
Afiliação
  • Maggi L; Neuroimmunology and Neuromuscular Disease Unit, Foundation IRCCS Carlo Besta Neurological Institute, Milano, Italy lorenzo.maggi@istituto-besta.it.
  • Bello L; Department of Neurosciences, University of Padua, Padova, Veneto, Italy.
  • Bonanno S; Neuroimmunology and Neuromuscular Disease Unit, Foundation IRCCS Carlo Besta Neurological Institute, Milano, Italy.
  • Govoni A; Neuromuscular and Rare Disease Unit, La Fondazione IRCCS Ca' Granda Ospedale Maggiore di Milano Policlinico, Milano, Italy.
  • Caponnetto C; Department of Clinical and Experimental Medicine, University of Pisa, Pisa, Italy.
  • Passamano L; IRCCS AOU San Martino, Genova, Liguria, Italy.
  • Grandis M; Cardiomyology and Medical Genetics Unit, Università degli Studi della Campania Luigi Vanvitelli Scuola di Medicina e Chirurgia, Napoli, Campania, Italy.
  • Trojsi F; IRCCS AOU San Martino, Genova, Liguria, Italy.
  • Cerri F; Department of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genoa, Genova, Italy.
  • Ferraro M; First Division of Neurology, Department of Advanced Medical and Surgical Sciences, Università degli Studi della Campania Luigi Vanvitelli Scuola di Medicina e Chirurgia, Napoli, Campania, Italy.
  • Bozzoni V; Division of Neuroscience, Department of Neurology & INSPE, San Raffaele Hospital, Milano, Lombardia, Italy.
  • Caumo L; Department of Neurosciences Rita Levi Montalcini, Università degli Studi di Torino, Torino, Piemonte, Italy.
  • Piras R; Department of Neurosciences, University of Padua, Padova, Veneto, Italy.
  • Tanel R; Department of Neurosciences, University of Padua, Padova, Veneto, Italy.
  • Saccani E; ATS Sardegna, Carbonia, Sardegna, Italy.
  • Meneri M; U.O. Neurologia, Presidio Ospedaliero Santa Chiara, Trento, Trentino-Alto Adige, Italy.
  • Vacchiano V; Specialistic Medicine Unit, Azienda Ospedaliero-Universitaria di Parma, Parma, Emilia-Romagna, Italy.
  • Ricci G; Neuromuscular and Rare Disease Unit, La Fondazione IRCCS Ca' Granda Ospedale Maggiore di Milano Policlinico, Milano, Italy.
  • Soraru' G; UOC Clinica Neurologica, IRCCS Institute of Neurological Sciences of Bologna, Bologna, Emilia-Romagna, Italy.
  • D'Errico E; Department of Clinical and Experimental Medicine, University of Pisa, Pisa, Italy.
  • Tramacere I; Department of Neurosciences, University of Padua, Padova, Veneto, Italy.
  • Bortolani S; Department of Basic Medical Science, Neuroscience and Sense Organs, Università degli Studi di Bari, Bari, Puglia, Italy.
  • Pavesi G; Department of Research and Clinical Development, Scientific Directorate, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milano, Lombardia, Italy.
  • Zanin R; Department of Neurosciences Rita Levi Montalcini, Università degli Studi di Torino, Torino, Piemonte, Italy.
  • Silvestrini M; Neurosciences, University of Parma, Parma, Emilia-Romagna, Italy.
  • Politano L; Developmental Neurology, Foundation IRCCS Carlo Besta Neurological Institute, Milano, Italy.
  • Schenone A; Department of Experimental and Clinical Medicine, Universita Politecnica delle Marche Facolta di Medicina e Chirurgia, Ancona, Italy.
  • Previtali SC; Department of Neurological Sciences, AOU Ospedali Riuniti di Ancona, Ancona, Marche, Italy.
  • Berardinelli A; Cardiomyology and Medical Genetics Unit, Università degli Studi della Campania Luigi Vanvitelli Scuola di Medicina e Chirurgia, Napoli, Campania, Italy.
  • Turri M; IRCCS AOU San Martino, Genova, Liguria, Italy.
  • Verriello L; Department of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genoa, Genova, Italy.
  • Coccia M; Division of Neuroscience, Department of Neurology & INSPE, San Raffaele Hospital, Milano, Lombardia, Italy.
  • Mantegazza R; Department of Child Neuropsychiatry, Fondazione Istituto Neurologico Nazionale C Mondino Istituto di Ricovero e Cura a Carattere Scientifico, Pavia, Lombardia, Italy.
  • Liguori R; Department of Neurology/Stroke Unit, Bolzano Hospital, Bolzano, Trentino-Alto Adige, Italy.
  • Filosto M; Neurology Unit, Department of Neurosciences, University Hospital Santa Maria della Misericordia, Udine, Friuli-Venezia Giulia, Italy.
  • Marrosu G; Department of Neurological Sciences, AOU Ospedali Riuniti di Ancona, Ancona, Marche, Italy.
  • Siciliano G; Neuroimmunology and Neuromuscular Disease Unit, Foundation IRCCS Carlo Besta Neurological Institute, Milano, Italy.
  • Simone IL; UOC Clinica Neurologica, IRCCS Institute of Neurological Sciences of Bologna, Bologna, Emilia-Romagna, Italy.
  • Mongini T; Department of Biomedical and Neuromotor Sciences, Universita degli Studi di Bologna, Bologna, Italy.
  • Comi G; ERN-EURO NMD Center for Neuromuscular Diseases and Unit of Neurology, Azienda Ospedaliera Spedali Civili di Brescia, Brescia, Lombardia, Italy.
  • Pegoraro E; University of Brescia, Brescia, Italy.
J Neurol Neurosurg Psychiatry ; 91(11): 1166-1174, 2020 11.
Article em En | MEDLINE | ID: mdl-32917822

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Atrofias Musculares Espinais da Infância / Oligonucleotídeos Antissenso Tipo de estudo: Etiology_studies / Incidence_studies / Observational_studies / Risk_factors_studies Limite: Adolescent / Adult / Aged / Female / Humans / Male / Middle aged País/Região como assunto: Europa Idioma: En Revista: J Neurol Neurosurg Psychiatry Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Itália

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Atrofias Musculares Espinais da Infância / Oligonucleotídeos Antissenso Tipo de estudo: Etiology_studies / Incidence_studies / Observational_studies / Risk_factors_studies Limite: Adolescent / Adult / Aged / Female / Humans / Male / Middle aged País/Região como assunto: Europa Idioma: En Revista: J Neurol Neurosurg Psychiatry Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Itália