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Changes in PCSK 9 and apolipoprotein B100 in Niemann-Pick disease after enzyme replacement therapy with olipudase alfa.
Garside, Bethanie; Ho, Jan Hoong; Kwok, See; Liu, Yifen; Dhage, Shaishav; Donn, Rachelle; Iqbal, Zohaib; Jones, Simon A; Soran, Handrean.
Afiliação
  • Garside B; Lipid Research Group, Division of Cardiovascular Sciences, University of Manchester, Manchester, UK.
  • Ho JH; Lipid Research Group, Division of Cardiovascular Sciences, University of Manchester, Manchester, UK.
  • Kwok S; Cardiovascular Trials Unit, Manchester Royal Infirmary, Manchester University NHS Foundation Trust, Oxford Road, Manchester, M13 9WL, UK.
  • Liu Y; Lipid Research Group, Division of Cardiovascular Sciences, University of Manchester, Manchester, UK.
  • Dhage S; Lipid Research Group, Division of Cardiovascular Sciences, University of Manchester, Manchester, UK.
  • Donn R; Cardiovascular Trials Unit, Manchester Royal Infirmary, Manchester University NHS Foundation Trust, Oxford Road, Manchester, M13 9WL, UK.
  • Iqbal Z; Faculty of Biology, Medicine and Health, University of Manchester, Manchester, UK.
  • Jones SA; Lipid Research Group, Division of Cardiovascular Sciences, University of Manchester, Manchester, UK.
  • Soran H; Cardiovascular Trials Unit, Manchester Royal Infirmary, Manchester University NHS Foundation Trust, Oxford Road, Manchester, M13 9WL, UK.
Orphanet J Rare Dis ; 16(1): 107, 2021 02 27.
Article em En | MEDLINE | ID: mdl-33639994

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Esfingomielina Fosfodiesterase / Doença de Niemann-Pick Tipo A / Apolipoproteína B-100 / Terapia de Reposição de Enzimas / Pró-Proteína Convertase 9 Limite: Adult / Humans Idioma: En Revista: Orphanet J Rare Dis Assunto da revista: MEDICINA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Esfingomielina Fosfodiesterase / Doença de Niemann-Pick Tipo A / Apolipoproteína B-100 / Terapia de Reposição de Enzimas / Pró-Proteína Convertase 9 Limite: Adult / Humans Idioma: En Revista: Orphanet J Rare Dis Assunto da revista: MEDICINA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Reino Unido