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Azacitidine for patients with Vacuoles, E1 Enzyme, X-linked, Autoinflammatory, Somatic syndrome (VEXAS) and myelodysplastic syndrome: data from the French VEXAS registry.
Comont, Thibault; Heiblig, Mael; Rivière, Etienne; Terriou, Louis; Rossignol, Julien; Bouscary, Didier; Rieu, Virginie; Le Guenno, Guillaume; Mathian, Alexis; Aouba, Achille; Vinit, Julien; Dion, Jeremie; Kosmider, Olivier; Terrier, Benjamin; Georgin-Lavialle, Sophie; Fenaux, Pierre; Mekinian, Arsène.
Afiliação
  • Comont T; Department of Internal Medicine, IUCT-Oncopole, University Hospital of Toulouse, Université Toulouse III - Paul Sabatier, Toulouse, France.
  • Heiblig M; Department of Hematology, Lyon-Sud Hospital, Hospices Civils de Lyon, Université Lyon Sud, Pierre Bénite, France.
  • Rivière E; Department of Internal Medicine, University of Bordeaux, Haut-Lévêque Hospital, Pessac, France.
  • Terriou L; Department of Internal Medicine and Clinical Immunology, University of Lille, CHU Lille, Lille, France.
  • Rossignol J; French Reference Center for Mastocytosis (CEREMAST), Hôpital Necker, Assistance Publique-Hôpitaux de Paris (APH-HP), Université de Paris, Paris, France.
  • Bouscary D; Departement of Hematology, Hôpital Cochin, Assistance Publique-Hôpitaux de Paris (APH-HP), Université de Paris, Paris, France.
  • Rieu V; Department of Internal Medicine, University Hospital Estaing, Université de Clermont-Ferrand, Clermont-Ferrand, France.
  • Le Guenno G; Department of Internal Medicine, University Hospital Estaing, Université de Clermont-Ferrand, Clermont-Ferrand, France.
  • Mathian A; Department of Internal Medicine, Pitie-Salpetriere Hospital, Assistance Publique-Hôpitaux de Paris (AP-HP), Université de Paris, Paris, France.
  • Aouba A; Department of Clinical Immunology and Internal Medicine, CHU of Caen Normandie, Université de Caen, Caen, France.
  • Vinit J; Department of Internal Medicine, CHWM, Chalon-sur-Saône, France.
  • Dion J; Department of Internal Medicine, IUCT-Oncopole, University Hospital of Toulouse, Université Toulouse III - Paul Sabatier, Toulouse, France.
  • Kosmider O; Hematology laboratory, Hôpital Cochin, Assistance Publique-Hôpitaux de Paris (APH-HP), Université de Paris, Paris, France.
  • Terrier B; Department of Internal Medicine, Hôpital Cochin, Assistance Publique-Hôpitaux de Paris (AP-HP), Université de Paris, Paris, France.
  • Georgin-Lavialle S; Department of Internal Medicine, Assistance Publique Hôpitaux de Paris (AP-HP), Tenon Hospital, National reference center for autoinflammatory diseases and AA amyloidosis (CEREMAIA), Sorbonne University, Université de Paris, Paris, France.
  • Fenaux P; Department of Hematology, Hopital Saint-Louis, Assistance Publique Hôpitaux de Paris (AP-HP), Université de Paris, Paris, France.
  • Mekinian A; Department of Internal Medicine, Assistance Publique Hôpitaux de Paris (AP-HP), Hôpital Saint-Antoine, Sorbonne University, Paris, France.
Br J Haematol ; 196(4): 969-974, 2022 02.
Article em En | MEDLINE | ID: mdl-34651299

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Dermatopatias Genéticas / Azacitidina / Síndromes Mielodisplásicas / Doenças Genéticas Ligadas ao Cromossomo X / Genes Ligados ao Cromossomo X / Antimetabólitos Antineoplásicos Limite: Aged / Female / Humans / Male / Middle aged País/Região como assunto: Europa Idioma: En Revista: Br J Haematol Ano de publicação: 2022 Tipo de documento: Article País de afiliação: França

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Dermatopatias Genéticas / Azacitidina / Síndromes Mielodisplásicas / Doenças Genéticas Ligadas ao Cromossomo X / Genes Ligados ao Cromossomo X / Antimetabólitos Antineoplásicos Limite: Aged / Female / Humans / Male / Middle aged País/Região como assunto: Europa Idioma: En Revista: Br J Haematol Ano de publicação: 2022 Tipo de documento: Article País de afiliação: França