Detalles de la búsqueda
1.
Large-scale purification of functional AAV particles packaging the full genome using short-term ultracentrifugation with a zonal rotor.
Gene Ther;
30(7-8): 641-648, 2023 08.
Artículo
en Inglés
| MEDLINE | ID: mdl-36977769
2.
Therapeutic Application of Extracellular Vesicles-Capsulated Adeno-Associated Virus Vector via nSMase2/Smpd3, Satellite, and Immune Cells in Duchenne Muscular Dystrophy.
Int J Mol Sci;
23(3)2022 Jan 28.
Artículo
en Inglés
| MEDLINE | ID: mdl-35163475
3.
High-Level Expression of Alkaline Phosphatase by Adeno-Associated Virus Vector Ameliorates Pathological Bone Structure in a Hypophosphatasia Mouse Model.
Calcif Tissue Int;
106(6): 665-677, 2020 06.
Artículo
en Inglés
| MEDLINE | ID: mdl-32076747
4.
Tyrosine triple mutated AAV2-BDNF gene therapy in a rat model of transient IOP elevation.
Mol Vis;
22: 816-26, 2016.
Artículo
en Inglés
| MEDLINE | ID: mdl-27440998
5.
Intrathecal AAV serotype 9-mediated delivery of shRNA against TRPV1 attenuates thermal hyperalgesia in a mouse model of peripheral nerve injury.
Mol Ther;
22(2): 409-419, 2014 Feb.
Artículo
en Inglés
| MEDLINE | ID: mdl-24322332
6.
Intraperitoneal administration of AAV9-shRNA inhibits target gene expression in the dorsal root ganglia of neonatal mice.
Mol Pain;
9: 36, 2013 Jul 18.
Artículo
en Inglés
| MEDLINE | ID: mdl-23866078
7.
Non-human primate model of amyotrophic lateral sclerosis with cytoplasmic mislocalization of TDP-43.
Brain;
135(Pt 3): 833-46, 2012 Mar.
Artículo
en Inglés
| MEDLINE | ID: mdl-22252998
8.
Intraperitoneal AAV9-shRNA inhibits target expression in neonatal skeletal and cardiac muscles.
Biochem Biophys Res Commun;
405(2): 204-9, 2011 Feb 11.
Artículo
en Inglés
| MEDLINE | ID: mdl-21219850
9.
Direct comparison of four adeno-associated virus serotypes in mediating the production of antiangiogenic proteins in mouse muscle.
Cancer Invest;
29(5): 353-9, 2011 Jun.
Artículo
en Inglés
| MEDLINE | ID: mdl-21599511
10.
Long-term inhibition of glycosphingolipid accumulation in Fabry model mice by a single systemic injection of AAV1 vector in the neonatal period.
Mol Genet Metab;
96(3): 91-6, 2009 Mar.
Artículo
en Inglés
| MEDLINE | ID: mdl-19091614
11.
Infectivity Assessment of Recombinant Adeno-Associated Virus and Wild-Type Adeno-Associated Virus Exposed to Various Diluents and Environmental Conditions.
Hum Gene Ther Methods;
30(4): 137-143, 2019 08.
Artículo
en Inglés
| MEDLINE | ID: mdl-31317781
12.
AAV1 mediated co-expression of formylglycine-generating enzyme and arylsulfatase a efficiently corrects sulfatide storage in a mouse model of metachromatic leukodystrophy.
Mol Ther;
15(1): 38-43, 2007 Jan.
Artículo
en Inglés
| MEDLINE | ID: mdl-17164773
13.
Highly Efficient Ultracentrifugation-free Chromatographic Purification of Recombinant AAV Serotype 9.
Mol Ther Methods Clin Dev;
11: 180-190, 2018 Dec 14.
Artículo
en Inglés
| MEDLINE | ID: mdl-30533449
14.
Ultracentrifugation-free chromatography-mediated large-scale purification of recombinant adeno-associated virus serotype 1 (rAAV1).
Mol Ther Methods Clin Dev;
3: 15058, 2016.
Artículo
en Inglés
| MEDLINE | ID: mdl-26913289
15.
Treatment of hypophosphatasia by muscle-directed expression of bone-targeted alkaline phosphatase via self-complementary AAV8 vector.
Mol Ther Methods Clin Dev;
3: 15059, 2016.
Artículo
en Inglés
| MEDLINE | ID: mdl-26904710
16.
Coexpression of formylglycine-generating enzyme is essential for synthesis and secretion of functional arylsulfatase A in a mouse model of metachromatic leukodystrophy.
Hum Gene Ther;
16(8): 929-36, 2005 Aug.
Artículo
en Inglés
| MEDLINE | ID: mdl-16076251
17.
Cardiovascular manifestations of Fabry disease and the novel therapeutic strategies.
J Nippon Med Sch;
72(5): 254-61, 2005 Oct.
Artículo
en Inglés
| MEDLINE | ID: mdl-16247224
18.
Enzyme replacement in the CSF to treat metachromatic leukodystrophy in mouse model using single intracerebroventricular injection of self-complementary AAV1 vector.
Sci Rep;
5: 13104, 2015 Aug 18.
Artículo
en Inglés
| MEDLINE | ID: mdl-26283284
19.
Targeted gene transfer into ependymal cells through intraventricular injection of AAV1 vector and long-term enzyme replacement via the CSF.
Sci Rep;
4: 5506, 2014 Jul 01.
Artículo
en Inglés
| MEDLINE | ID: mdl-24981028
20.
Serotype-independent method of recombinant adeno-associated virus (AAV) vector production and purification.
J Nippon Med Sch;
79(6): 394-402, 2012.
Artículo
en Inglés
| MEDLINE | ID: mdl-23291836