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Antisense Oligonucleotide-mediated Exon Skipping as a Systemic Therapeutic Approach for Recessive Dystrophic Epidermolysis Bullosa.
Bremer, Jeroen; Bornert, Olivier; Nyström, Alexander; Gostynski, Antoni; Jonkman, Marcel F; Aartsma-Rus, Annemieke; van den Akker, Peter C; Pasmooij, Anna Mg.
Afiliación
  • Bremer J; Department of Dermatology, University Medical Center Groningen, University of Groningen, Groningen, the Netherlands.
  • Bornert O; Department of Dermatology, Medical Center - University of Freiburg, Freiburg, Germany.
  • Nyström A; Department of Dermatology, Medical Center - University of Freiburg, Freiburg, Germany.
  • Gostynski A; Department of Dermatology, University Medical Center Groningen, University of Groningen, Groningen, the Netherlands.
  • Jonkman MF; Department of Dermatology, University Medical Center Groningen, University of Groningen, Groningen, the Netherlands.
  • Aartsma-Rus A; Department of Human Genetics, Leiden University Medical Center, Leiden, the Netherlands.
  • van den Akker PC; Department of Dermatology, University Medical Center Groningen, University of Groningen, Groningen, the Netherlands.
  • Pasmooij AM; Department of Genetics, University Medical Center Groningen, University of Groningen, Groningen, the Netherlands.
Mol Ther Nucleic Acids ; 5(10): e379, 2016 Oct 18.
Article en En | MEDLINE | ID: mdl-27754488

Texto completo: 1 Bases de datos: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Año: 2016 Tipo del documento: Article País de afiliación: Países Bajos

Texto completo: 1 Bases de datos: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Año: 2016 Tipo del documento: Article País de afiliación: Países Bajos