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Design of the DREPAGREFFE trial: A prospective controlled multicenter study evaluating the benefit of genoidentical hematopoietic stem cell transplantation over chronic transfusion in sickle cell anemia children detected to be at risk of stroke by transcranial Doppler (NCT 01340404).
Chevret, Sylvie; Verlhac, Suzanne; Ducros-Miralles, Elisabeth; Dalle, Jean-Hugues; de Latour, Regis Peffault; de Montalembert, Mariane; Benkerrou, Malika; Pondarré, Corinne; Thuret, Isabelle; Guitton, Corinne; Lesprit, Emmanuelle; Etienne-Julan, Maryse; Elana, Gisèle; Vannier, Jean-Pierre; Lutz, Patrick; Neven, Bénédicte; Galambrun, Claire; Paillard, Catherine; Runel, Camille; Jubert, Charlotte; Arnaud, Cécile; Kamdem, Annie; Brousse, Valentine; Missud, Florence; Petras, Marie; Doumdo-Divialle, Lydia; Berger, Claire; Fréard, Françoise; Taieb, Olivier; Drain, Elise; Elmaleh, Monique; Vasile, Manuela; Khelif, Yacine; Bernaudin, Myriam; Chadebech, Philippe; Pirenne, France; Socié, Gérard; Bernaudin, Françoise.
Afiliación
  • Chevret S; Statistical, Methodology Department, Paris-St-Louis Hospital, Paris-Diderot University, France. Electronic address: sylvie.chevret@paris7.jussieu.fr.
  • Verlhac S; Medical Imaging Department, Referral Center for Sickle Cell Disease, Créteil-CHIC Hospital, Créteil, France; Pediatric Imaging Department, Robert-Debré Hospital, Paris-Diderot University, France. Electronic address: suzanne.verlhac@chicreteil.fr.
  • Ducros-Miralles E; Pediatric Department, Referral Center for Sickle Cell Disease, Créteil-CHIC Hospital, Paris-Est University, Créteil, France. Electronic address: ducros.miralles@free.fr.
  • Dalle JH; Pediatric Hematology Department, Paris-Debré Hospital, Paris-Diderot University, France. Electronic address: jean-hugues.dalle@aphp.fr.
  • de Latour RP; Hematology Department, Paris-St-Louis Hospital, Paris-Diderot University, France. Electronic address: regis.peffaultdelatour@aphp.fr.
  • de Montalembert M; Pediatric Department, Referral Center for Sickle Cell Disease, Paris-Necker Hospital, Paris-Descartes University, France. Electronic address: mariane.demontal@aphp.fr.
  • Benkerrou M; Pediatric Department, Referral Center for Sickle Cell Disease, Paris-Debré Hospital, Paris-Diderot University, France. Electronic address: malika.benkerrou@aphp.fr.
  • Pondarré C; Pediatric Hematology Department, Lyon Léon Bérard Center, Lyon, France; Pediatric Department, Referral Center for Sickle Cell Disease, Créteil-CHIC Hospital, Paris-Est University, Créteil, France. Electronic address: corinne.pondarre@chicreteil.fr.
  • Thuret I; Pediatric Hematology Department, Marseille-la Timone Hospital, Aix-Marseille University, France. Electronic address: Isabelle.THURET@ap-hm.fr.
  • Guitton C; Pediatric Department, Referral Center for Sickle Cell Disease, Bicêtre Hospital, Paris-Sud University, France. Electronic address: corinne.guitton@aphp.fr.
  • Lesprit E; Pediatric Department, Referral Center for Sickle Cell Disease, Paris-Trousseau Hospital, Paris-Diderot University, France. Electronic address: emmanuelle.lesprit@aphp.fr.
  • Etienne-Julan M; Referral Center for Sickle Cell Disease, Pointe à Pitre Hospital, Antilles University, Guadeloupe, France. Electronic address: maryse.etienne-julan@chu-guadeloupe.fr.
  • Elana G; Pediatric Department, Referral Center for Sickle Cell Disease, Fort de France Hospital, Antilles University, Martinique, France. Electronic address: gisele.elana@chu-fortdefrance.fr.
  • Vannier JP; Pediatric Hematology Department, Rouen-Charles-Nicolle Hospital, Rouen University, France. Electronic address: Jean-Pierre.Vannier@chu-rouen.fr.
  • Lutz P; Pediatric Onco-Hematology Department, Strasbourg-Hautepierre Hospital, Strasbourg University, France. Electronic address: Patrick.Lutz@chru-strasbourg.fr.
  • Neven B; Pediatric Immuno-Hematology Department, Paris-Necker Hospital, Paris-Descartes University, France. Electronic address: Benedicte.neven@aphp.fr.
  • Galambrun C; Pediatric Hematology Department, Marseille-la Timone Hospital, Aix-Marseille University, France. Electronic address: Claire.GALAMBRUN@ap-hm.fr.
  • Paillard C; Pediatric Onco-Hematology Department, Strasbourg-Hautepierre Hospital, Strasbourg University, France. Electronic address: catherine.paillard@chru-strasbourg.fr.
  • Runel C; Pediatric Hematology Department, Bordeaux-Hospital, Bordeaux University, France. Electronic address: camille.runel@chu-bordeaux.fr.
  • Jubert C; Pediatric Hematology Department, Bordeaux-Hospital, Bordeaux University, France. Electronic address: charlotte.jubert@chu-bordeaux.fr.
  • Arnaud C; Pediatric Department, Referral Center for Sickle Cell Disease, Créteil-CHIC Hospital, Paris-Est University, Créteil, France. Electronic address: cecile.arnaud@chicreteil.fr.
  • Kamdem A; Pediatric Department, Referral Center for Sickle Cell Disease, Créteil-CHIC Hospital, Paris-Est University, Créteil, France. Electronic address: annie.kamdem@chicreteil.fr.
  • Brousse V; Pediatric Department, Referral Center for Sickle Cell Disease, Paris-Necker Hospital, Paris-Descartes University, France. Electronic address: valentine.brousse@chicreteil.fr.
  • Missud F; Pediatric Department, Referral Center for Sickle Cell Disease, Paris-Debré Hospital, Paris-Diderot University, France. Electronic address: florence.missud@aphp.fr.
  • Petras M; Referral Center for Sickle Cell Disease, Pointe à Pitre Hospital, Antilles University, Guadeloupe, France. Electronic address: eleonore.petras@chu-guadeloupe.fr.
  • Doumdo-Divialle L; Referral Center for Sickle Cell Disease, Pointe à Pitre Hospital, Antilles University, Guadeloupe, France. Electronic address: lydia-divialle.doumdo@chu-guadeloupe.fr.
  • Berger C; Onco-Hematology Department, St-Etienne Hospital, St-Etienne University, France. Electronic address: claire.berger@chu-st-etienne.fr.
  • Fréard F; Pediatric Department, Referral Center for Sickle Cell Disease, Créteil-CHIC Hospital, Paris-Est University, Créteil, France. Electronic address: francoise.freard@wanadoo.fr.
  • Taieb O; Ethno-Psychiatry Department, Avicenne-Hospital, Paris-13 University, France. Electronic address: olivier.taieb@aphp.fr.
  • Drain E; Ethno-Psychiatry Department, Avicenne-Hospital, Paris-13 University, France. Electronic address: elise.drain@aphp.fr.
  • Elmaleh M; Pediatric Imaging Department, Robert-Debré Hospital, Paris-Diderot University, France. Electronic address: monique.elmaleh@aphp.fr.
  • Vasile M; Pediatric Imaging Department, Robert-Debré Hospital, Paris-Diderot University, France. Electronic address: Manuela.Vasile@chicreteil.fr.
  • Khelif Y; Normandie Univ, UNICAEN, CEA, CNRS, ISTCT/CERVOxy group, 14000 Caen, France. Electronic address: khelif@cyceron.Fr.
  • Bernaudin M; Normandie Univ, UNICAEN, CEA, CNRS, ISTCT/CERVOxy group, 14000 Caen, France. Electronic address: bernaudin@cyceron.Fr.
  • Chadebech P; EFS Ile de France, IMRB INSERM U955 équipe 2 (Créteil), GR-Ex (Paris) and Paris-Est-Créteil University, France. Electronic address: philippe.chadebech@efs.sante.fr.
  • Pirenne F; EFS Ile de France, IMRB INSERM U955 équipe 2 (Créteil), GR-Ex (Paris) and Paris-Est-Créteil University, France. Electronic address: france.pirenne@efs.sante.fr.
  • Socié G; Hematology Department, Paris-St-Louis Hospital, Paris-Diderot University, France. Electronic address: gerard.socie@aphp.fr.
  • Bernaudin F; Pediatric Department, Referral Center for Sickle Cell Disease, Créteil-CHIC Hospital, Paris-Est University, Créteil, France. Electronic address: Francoise.Bernaudin@chicreteil.fr.
Contemp Clin Trials ; 62: 91-104, 2017 11.
Article en En | MEDLINE | ID: mdl-28821470

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Trasplante de Células Madre Hematopoyéticas / Accidente Cerebrovascular / Reacción a la Transfusión / Anemia de Células Falciformes Tipo de estudio: Clinical_trials / Etiology_studies / Observational_studies / Risk_factors_studies Límite: Adolescent / Child / Child, preschool / Female / Humans / Male Idioma: En Revista: Contemp Clin Trials Asunto de la revista: MEDICINA / TERAPEUTICA Año: 2017 Tipo del documento: Article

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Trasplante de Células Madre Hematopoyéticas / Accidente Cerebrovascular / Reacción a la Transfusión / Anemia de Células Falciformes Tipo de estudio: Clinical_trials / Etiology_studies / Observational_studies / Risk_factors_studies Límite: Adolescent / Child / Child, preschool / Female / Humans / Male Idioma: En Revista: Contemp Clin Trials Asunto de la revista: MEDICINA / TERAPEUTICA Año: 2017 Tipo del documento: Article