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Deep characterization of the anti-drug antibodies developed in Fabry disease patients, a prospective analysis from the French multicenter cohort FFABRY.
Mauhin, Wladimir; Lidove, Olivier; Amelin, Damien; Lamari, Foudil; Caillaud, Catherine; Mingozzi, Federico; Dzangué-Tchoupou, Gaëlle; Arouche-Delaperche, Louiza; Douillard, Claire; Dussol, Bertrand; Leguy-Seguin, Vanessa; D'Halluin, Pauline; Noel, Esther; Zenone, Thierry; Matignon, Marie; Maillot, François; Ly, Kim-Heang; Besson, Gérard; Willems, Marjolaine; Labombarda, Fabien; Masseau, Agathe; Lavigne, Christian; Froissart, Roseline; Lacombe, Didier; Ziza, Jean Marc; Hachulla, Eric; Benveniste, Olivier.
Afiliación
  • Mauhin W; Sorbonne Université, INSERM, UMR 974, Centre of Research in Myology, Association Institut de Myologie, Pitié-Salpêtrière University Hospital, 75013, Paris, France. wladimir.mauhin@aphp.fr.
  • Lidove O; Sorbonne Université, INSERM, UMR 974, Centre of Research in Myology, Association Institut de Myologie, Pitié-Salpêtrière University Hospital, 75013, Paris, France.
  • Amelin D; Internal Medicine and Rheumatology Department, Diaconesses-Croix Saint Simon Hospital Group, Paris, France.
  • Lamari F; Sorbonne Université, INSERM, UMR 974, Centre of Research in Myology, Association Institut de Myologie, Pitié-Salpêtrière University Hospital, 75013, Paris, France.
  • Caillaud C; Metabolic Biochemistry Department, Pitié Salpêtrière University Hospital, AP-HP, Paris, France.
  • Mingozzi F; GRC13-Neurometabolisme- Sorbonne Universités UPMC, Paris 06, Paris, France.
  • Dzangué-Tchoupou G; Biochemistry, Metabolomic and Proteomic Department, Necker Enfants Malades University Hospital, AP-HP, Paris, France.
  • Arouche-Delaperche L; INSERM U1151, Institute Necker Enfants Malades, Paris Descartes University, Paris, France.
  • Douillard C; Sorbonne Université, INSERM, UMR 974, Centre of Research in Myology, Association Institut de Myologie, Pitié-Salpêtrière University Hospital, 75013, Paris, France.
  • Dussol B; Sorbonne Université, INSERM, UMR 974, Centre of Research in Myology, Association Institut de Myologie, Pitié-Salpêtrière University Hospital, 75013, Paris, France.
  • Leguy-Seguin V; Sorbonne Université, INSERM, UMR 974, Centre of Research in Myology, Association Institut de Myologie, Pitié-Salpêtrière University Hospital, 75013, Paris, France.
  • D'Halluin P; Reference Center for Inborn Metabolic diseases, Jeanne de Flandres Hospital, Lille, France.
  • Noel E; Nephrology Department, Aix Marseille Université et Centre d'Investigation Clinique 1409, INSERM/AMU/AP-HM, Marseille, France.
  • Zenone T; Internal Medicine and Clinical Immunology Department, Francois Mitterrand Hospital, Dijon, France.
  • Matignon M; Nephrology and Clinical Immunology Department, Tours University Hospital, François Rabelais University, Tours, France.
  • Maillot F; Internal Medicine Department, Strasbourg University Hospital, Strasbourg, France.
  • Ly KH; Internal Medicine Department, Valence Hospital, Valence, France.
  • Besson G; Nephrology and Renal Transplantation Department, Institut Francilien de Recherche en Néphrologie et Transplantation (IFRNT), Henri-Mondor/Albert-Chenevier University Hospital, APHP, Créteil, France.
  • Willems M; University of Paris-Est-Créteil (UPEC), DHU (Département Hospitalo-Universitaire) VIC (Virus-Immunité-Cancer), IMRB (Institut Mondor de Recherche Biomédicale), Team 21, INSERM U 955, Créteil, France.
  • Labombarda F; Internal Medicine Department, Tours University Hospital, University of Tours, UMR INSERM 1253, Tours, France.
  • Masseau A; Internal Medicine Department, Dupuytren University Hospital, Limoges, France.
  • Lavigne C; Neurology Department, Grenoble University Hospital, Grenoble, France.
  • Froissart R; Medical Genetics and Rare Diseases Department, Montpellier University Hospital, Montpellier, France.
  • Lacombe D; Cardiology Department, Caen University Hospital, Caen, France.
  • Ziza JM; Internal Medicine Department, Hôtel-Dieu University Hospital, Nantes, France.
  • Hachulla E; Internal Medicine and Vascular Diseases Department, Angers University Hospital, Angers, France.
  • Benveniste O; Laboratory for Inborn Errors of Metabolism, East Hospital, Hospices Civils de Lyon, Bron, France.
Orphanet J Rare Dis ; 13(1): 127, 2018 07 31.
Article en En | MEDLINE | ID: mdl-30064518

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Enfermedad de Fabry / Alfa-Galactosidasa / Anticuerpos Tipo de estudio: Clinical_trials / Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Límite: Adult / Female / Humans / Male / Middle aged Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2018 Tipo del documento: Article País de afiliación: Francia

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Enfermedad de Fabry / Alfa-Galactosidasa / Anticuerpos Tipo de estudio: Clinical_trials / Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Límite: Adult / Female / Humans / Male / Middle aged Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2018 Tipo del documento: Article País de afiliación: Francia