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Genome editing-mediated knock-in of therapeutic genes ameliorates the disease phenotype in a model of hemophilia.
Lee, Jeong Hyeon; Oh, Hye-Kyung; Choi, Beom Seok; Lee, Ho Hyeon; Lee, Kyu Jun; Kim, Un Gi; Lee, Jina; Lee, Hyerim; Lee, Geon Seong; Ahn, Se Jun; Han, Jeong Pil; Kim, Seokjoong; Yeom, Su Cheong; Song, Dong Woo.
Afiliación
  • Lee JH; Graduate School of International Agricultural Technology and Institute of Green-Bio Science and Technology, Seoul National University, 1447 Pyeongchang-Ro, Daewha, Pyeongchang, Gangwon 25354, Korea.
  • Oh HK; Research and Development Center, Toolgen Incorporated, Geumcheon-gu, Seoul 08501, Korea.
  • Choi BS; Research and Development Center, Toolgen Incorporated, Geumcheon-gu, Seoul 08501, Korea.
  • Lee HH; Research and Development Center, Toolgen Incorporated, Geumcheon-gu, Seoul 08501, Korea.
  • Lee KJ; Research and Development Center, Toolgen Incorporated, Geumcheon-gu, Seoul 08501, Korea.
  • Kim UG; Research and Development Center, Toolgen Incorporated, Geumcheon-gu, Seoul 08501, Korea.
  • Lee J; Research and Development Center, Toolgen Incorporated, Geumcheon-gu, Seoul 08501, Korea.
  • Lee H; Research and Development Center, Toolgen Incorporated, Geumcheon-gu, Seoul 08501, Korea.
  • Lee GS; Graduate School of International Agricultural Technology and Institute of Green-Bio Science and Technology, Seoul National University, 1447 Pyeongchang-Ro, Daewha, Pyeongchang, Gangwon 25354, Korea.
  • Ahn SJ; Graduate School of International Agricultural Technology and Institute of Green-Bio Science and Technology, Seoul National University, 1447 Pyeongchang-Ro, Daewha, Pyeongchang, Gangwon 25354, Korea.
  • Han JP; Graduate School of International Agricultural Technology and Institute of Green-Bio Science and Technology, Seoul National University, 1447 Pyeongchang-Ro, Daewha, Pyeongchang, Gangwon 25354, Korea.
  • Kim S; Research and Development Center, Toolgen Incorporated, Geumcheon-gu, Seoul 08501, Korea.
  • Yeom SC; Graduate School of International Agricultural Technology and Institute of Green-Bio Science and Technology, Seoul National University, 1447 Pyeongchang-Ro, Daewha, Pyeongchang, Gangwon 25354, Korea.
  • Song DW; WCU Biomodulation Major, Department of Agricultural Biotechnology, Seoul National University, Gwanank-gu, Seoul 08826, Korea.
Mol Ther Nucleic Acids ; 29: 551-562, 2022 Sep 13.
Article en En | MEDLINE | ID: mdl-36090746

Texto completo: 1 Bases de datos: MEDLINE Tipo de estudio: Prognostic_studies Idioma: En Revista: Mol Ther Nucleic Acids Año: 2022 Tipo del documento: Article

Texto completo: 1 Bases de datos: MEDLINE Tipo de estudio: Prognostic_studies Idioma: En Revista: Mol Ther Nucleic Acids Año: 2022 Tipo del documento: Article