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Enzyme replacement with transferrin receptor-targeted α-L-iduronidase rescues brain pathology in mucopolysaccharidosis I mice.
Kida, Sachiho; Koshimura, Yuri; Yoden, Eiji; Yoshioka, Aya; Morimoto, Hideto; Imakiire, Atsushi; Tanaka, Noboru; Tanaka, Satowa; Mori, Ayaka; Ito, Jun; Inoue, Asuka; Yamamoto, Ryuji; Minami, Kohtaro; Hirato, Tohru; Takahashi, Kenichi; Sonoda, Hiroyuki.
Afiliación
  • Kida S; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Koshimura Y; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Yoden E; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Yoshioka A; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Morimoto H; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Imakiire A; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Tanaka N; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Tanaka S; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Mori A; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Ito J; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Inoue A; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Yamamoto R; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Minami K; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Hirato T; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Takahashi K; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
  • Sonoda H; Research Division, JCR Pharmaceuticals, 1-5-4 Murotani, Nishi-ku, Kobe 651-2241, Japan.
Mol Ther Methods Clin Dev ; 29: 439-449, 2023 Jun 08.
Article en En | MEDLINE | ID: mdl-37251981

Texto completo: 1 Bases de datos: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Año: 2023 Tipo del documento: Article País de afiliación: Japón

Texto completo: 1 Bases de datos: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Año: 2023 Tipo del documento: Article País de afiliación: Japón