Detalhe da pesquisa
1.
Outcomes following treatment for ADA-deficient severe combined immunodeficiency: a report from the PIDTC.
Blood
; 140(7): 685-705, 2022 08 18.
Artigo
em Inglês
| MEDLINE | ID: mdl-35671392
2.
Improved Titer and Gene Transfer by Lentiviral Vectors Using Novel, Small ß-Globin Locus Control Region Elements.
Mol Ther
; 28(1): 328-340, 2020 01 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-31628051
3.
ß-Thalassemia: all about that base, no cutting.
Blood
; 141(10): 1098-1099, 2023 03 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-36893006
4.
Global and Local Manipulation of DNA Repair Mechanisms to Alter Site-Specific Gene Editing Outcomes in Hematopoietic Stem Cells.
Front Genome Ed
; 2: 601541, 2020.
Artigo
em Inglês
| MEDLINE | ID: mdl-34713224