Detalhe da pesquisa
1.
CD19/22 CAR T cells in children and young adults with B-ALL: phase 1 results and development of a novel bicistronic CAR.
Blood
; 140(5): 451-463, 2022 08 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-35605184
2.
Understanding chronic pain in Neurofibromatosis Type 1 using the Neurofibromatosis Pain Module (NFPM).
Am J Med Genet A
; 194(6): e63541, 2024 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-38234177
3.
Perceived transition readiness among adolescents and young adults with neurofibromatosis type 1 and plexiform neurofibromas: a cross-sectional descriptive study.
J Pediatr Psychol
; 2024 Feb 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-38366576
4.
Perspectives of adults with neurofibromatosis regarding the design of psychosocial trials: Results from an anonymous online survey.
Clin Trials
; 21(1): 73-84, 2024 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-37962219
5.
Development and pilot validation of a novel disfigurement severity scale for plexiform neurofibromas in children with neurofibromatosis type 1.
Clin Trials
; 21(2): 189-198, 2024 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-37877369
6.
Recommendations for assessing appearance concerns related to plexiform and cutaneous neurofibromas in neurofibromatosis 1 clinical trials.
Clin Trials
; 21(1): 6-17, 2024 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-38140900
7.
Selumetinib in Children with Inoperable Plexiform Neurofibromas.
N Engl J Med
; 382(15): 1430-1442, 2020 04 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-32187457
8.
Longitudinal association between executive function and academic achievement in children with neurofibromatosis type 1 and plexiform neurofibromas.
J Int Neuropsychol Soc
; 29(9): 839-849, 2023 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-36750981
9.
Longitudinal neurocognitive effects of nonmyeloablative hematopoietic stem cell transplant among older adolescents and adults with sickle cell disease: A description and comparison with sibling donors.
Neuropsychol Rehabil
; : 1-20, 2023 Aug 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-37540620
10.
Pharmacodynamic Study of Miransertib in Individuals with Proteus Syndrome.
Am J Hum Genet
; 104(3): 484-491, 2019 03 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-30803705
11.
Adolescents and young adults with neurofibromatosis type 1: A descriptive study of adaptive functioning.
Am J Med Genet A
; 188(2): 488-497, 2022 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-34731530
12.
Impact of the coronavirus pandemic on mental health and health care in adults with neurofibromatosis: Patient perspectives from an online survey.
Am J Med Genet A
; 188(1): 71-82, 2022 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-34536052
13.
Advancing RAS/RASopathy therapies: An NCI-sponsored intramural and extramural collaboration for the study of RASopathies.
Am J Med Genet A
; 182(4): 866-876, 2020 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-31913576
14.
Sleep disturbance in adults with sickle cell disease: relationships with executive and psychological functioning.
Ann Hematol
; 99(9): 2057-2064, 2020 Sep.
Artigo
em Inglês
| MEDLINE | ID: mdl-32458066
15.
Predictors of cognitive development in children with neurofibromatosis type 1 and plexiform neurofibromas.
Dev Med Child Neurol
; 62(8): 977-984, 2020 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-32052421
16.
Neurocognitive functioning in symptomatic adults with sickle cell disease: A description and comparison with unaffected siblings.
Neuropsychol Rehabil
; 30(9): 1666-1681, 2020 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-30924397
17.
Activity of Selumetinib in Neurofibromatosis Type 1-Related Plexiform Neurofibromas.
N Engl J Med
; 375(26): 2550-2560, 2016 12 29.
Artigo
em Inglês
| MEDLINE | ID: mdl-28029918
18.
2016 Children's Tumor Foundation conference on neurofibromatosis type 1, neurofibromatosis type 2, and schwannomatosis.
Am J Med Genet A
; 176(5): 1258-1269, 2018 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-29681099
19.
The Relationship Between Heart Rate Variability, Psychological Flexibility, and Pain in Neurofibromatosis Type 1.
Pain Pract
; 18(8): 969-978, 2018 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-29570943
20.
Treatment of HIV-associated primary CNS lymphoma with antiretroviral therapy, rituximab, and high-dose methotrexate.
Blood
; 136(19): 2229-2232, 2020 11 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-32609814