Detalhe da pesquisa
1.
Clinical outcome assessments of disease burden and progression in late-onset GM2 gangliosidoses.
Mol Genet Metab
; 142(3): 108512, 2024 Jun 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-38870773
2.
Venglustat combined with imiglucerase for neurological disease in adults with Gaucher disease type 3: the LEAP trial.
Brain
; 146(2): 461-474, 2023 02 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-36256599
3.
Venglustat, a Novel Glucosylceramide Synthase Inhibitor, in Patients at Risk of Rapidly Progressing ADPKD: Primary Results of a Double-Blind, Placebo-Controlled, Phase 2/3 Randomized Clinical Trial.
Am J Kidney Dis
; 81(5): 517-527.e1, 2023 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-36535535
4.
Reductions in Atherogenic Lipids and Major Cardiovascular Events: A Pooled Analysis of 10 ODYSSEY Trials Comparing Alirocumab With Control.
Circulation
; 134(24): 1931-1943, 2016 Dec 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-27777279
5.
Anticoagulation with otamixaban and ischemic events in non-ST-segment elevation acute coronary syndromes: the TAO randomized clinical trial.
JAMA
; 310(11): 1145-55, 2013 Sep 18.
Artigo
em Inglês
| MEDLINE | ID: mdl-23995608
6.
Safety and efficacy of venglustat in GBA1-associated Parkinson's disease: an international, multicentre, double-blind, randomised, placebo-controlled, phase 2 trial.
Lancet Neurol
; 22(8): 661-671, 2023 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-37479372
7.
The STAGED-PKD 2-Stage Adaptive Study With a Patient Enrichment Strategy and Treatment Effect Modeling for Improved Study Design Efficiency in Patients With ADPKD.
Kidney Med
; 4(10): 100538, 2022 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-36204243
8.
Safety, Pharmacokinetics, and Pharmacodynamics of Oral Venglustat in Patients with Parkinson's Disease and a GBA Mutation: Results from Part 1 of the Randomized, Double-Blinded, Placebo-Controlled MOVES-PD Trial.
J Parkinsons Dis
; 12(2): 557-570, 2022.
Artigo
em Inglês
| MEDLINE | ID: mdl-34897099
9.
Effects of a selective vasopressin V2 receptor antagonist, satavaptan, on ascites recurrence after paracentesis in patients with cirrhosis.
J Hepatol
; 53(2): 283-90, 2010 Aug.
Artigo
em Inglês
| MEDLINE | ID: mdl-20541828
10.
Lipoprotein(a) reductions from PCSK9 inhibition and major adverse cardiovascular events: Pooled analysis of alirocumab phase 3 trials.
Atherosclerosis
; 288: 194-202, 2019 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-31253441
11.
Effect of alirocumab dose increase on LDL lowering and lipid goal attainment in patients with dyslipidemia.
Coron Artery Dis
; 28(3): 190-197, 2017 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-27740972
12.
Effect of Alirocumab on Lipoprotein(a) Over ≥1.5 Years (from the Phase 3 ODYSSEY Program).
Am J Cardiol
; 119(1): 40-46, 2017 Jan 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-27793396
13.
Efficacy and safety of the proprotein convertase subtilisin/kexin type 9 monoclonal antibody alirocumab vs placebo in patients with heterozygous familial hypercholesterolemia.
J Clin Lipidol
; 11(1): 195-203.e4, 2017.
Artigo
em Inglês
| MEDLINE | ID: mdl-28391886
14.
Efficacy of alirocumab in high cardiovascular risk populations with or without heterozygous familial hypercholesterolemia: Pooled analysis of eight ODYSSEY Phase 3 clinical program trials.
Int J Cardiol
; 223: 750-757, 2016 Nov 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-27573600
15.
[Multiplicity of inferences in clinical trials: adjustment methods, clinical interpretation issues]. / Du bon usage des tests dans les essais cliniques.
Med Sci (Paris)
; 20(2): 231-5, 2004 Feb.
Artigo
em Francês
| MEDLINE | ID: mdl-14997445
16.
Economic Burden of Hepatitis in South Korea.
Jpn J Infect Dis
; 69(4): 354, 2016.
Artigo
em Inglês
| MEDLINE | ID: mdl-27534719
17.
Bleeding risk in patients with atrial fibrillation: the AMADEUS study.
Chest
; 140(1): 146-155, 2011 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-21415134
18.
Sensitivity analysis of longitudinal normal data with drop-outs.
Stat Med
; 23(7): 1039-54, 2004 Apr 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-15057877
19.
Sensitivity analysis of longitudinal binary data with non-monotone missing values.
Biostatistics
; 5(4): 531-44, 2004 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-15475417
20.
Long-term safety of fluticasone propionate and nedocromil sodium on bone in children with asthma.
Pediatrics
; 111(6 Pt 1): e706-13, 2003 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-12777589