Detalhe da pesquisa
1.
An empowered, clinically viable hematopoietic stem cell gene therapy for the treatment of multisystemic mucopolysaccharidosis type II.
Mol Ther
; 32(3): 619-636, 2024 Mar 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-38310355
2.
Prostaglandin E2 as transduction enhancer affects competitive engraftment of human hematopoietic stem and progenitor cells.
Mol Ther Methods Clin Dev
; 31: 101131, 2023 Dec 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-37920236
3.
A comprehensive single cell transcriptional landscape of human hematopoietic progenitors.
Nat Commun
; 10(1): 2395, 2019 06 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-31160568
4.
Intracerebroventricular delivery of hematopoietic progenitors results in rapid and robust engraftment of microglia-like cells.
Sci Adv
; 3(12): e1701211, 2017 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-29226242
5.
Design of a regulated lentiviral vector for hematopoietic stem cell gene therapy of globoid cell leukodystrophy.
Mol Ther Methods Clin Dev
; 2: 15038, 2015.
Artigo
em Inglês
| MEDLINE | ID: mdl-26509184