Detalhe da pesquisa
1.
Venglustat, a Novel Glucosylceramide Synthase Inhibitor, in Patients at Risk of Rapidly Progressing ADPKD: Primary Results of a Double-Blind, Placebo-Controlled, Phase 2/3 Randomized Clinical Trial.
Am J Kidney Dis
; 81(5): 517-527.e1, 2023 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-36535535
2.
The STAGED-PKD 2-Stage Adaptive Study With a Patient Enrichment Strategy and Treatment Effect Modeling for Improved Study Design Efficiency in Patients With ADPKD.
Kidney Med
; 4(10): 100538, 2022 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-36204243
3.
Patients with Protein-Truncating PKD1 Mutations and Mild ADPKD.
Clin J Am Soc Nephrol
; 16(3): 374-383, 2021 03 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-33602752