Detalhe da pesquisa
1.
Extracellular communication between brain cells through functional transfer of Cre mRNA mediated by extracellular vesicles.
Mol Ther
; 31(7): 2220-2239, 2023 07 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-37194237
2.
Retinal Organoids from an AIPL1 CRISPR/Cas9 Knockout Cell Line Successfully Recapitulate the Molecular Features of LCA4 Disease.
Int J Mol Sci
; 24(6)2023 Mar 21.
Artigo
em Inglês
| MEDLINE | ID: mdl-36982987
3.
A Novel Genetic Variant in MBD5 Associated with Severe Epilepsy and Intellectual Disability: Potential Implications on Neural Primary Cilia.
Int J Mol Sci
; 24(16)2023 Aug 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-37628781
4.
Induced Pluripotent Stem Cells and Genome-Editing Tools in Determining Gene Function and Therapy for Inherited Retinal Disorders.
Int J Mol Sci
; 23(23)2022 Dec 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-36499601
5.
Inhibition of HIV replication through siRNA carried by CXCR4-targeted chimeric nanobody.
Cell Mol Life Sci
; 77(14): 2859-2870, 2020 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-31641784
6.
Gene and Cell Therapy for AIPL1-Associated Leber Congenital Amaurosis: Challenges and Prospects.
Adv Exp Med Biol
; 1185: 97-101, 2019.
Artigo
em Inglês
| MEDLINE | ID: mdl-31884595
7.
Effective AAV-mediated gene replacement therapy in retinal organoids modeling AIPL1-associated LCA4.
Mol Ther Nucleic Acids
; 35(1): 102148, 2024 Mar 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-38439910
8.
Exploring the potential of cell-derived vesicles for transient delivery of gene editing payloads.
Adv Drug Deliv Rev
; : 115346, 2024 Jun 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-38849005
9.
Astrocyte-induced synaptogenesis is mediated by transforming growth factor ß signaling through modulation of D-serine levels in cerebral cortex neurons.
J Biol Chem
; 287(49): 41432-45, 2012 Nov 30.
Artigo
em Inglês
| MEDLINE | ID: mdl-23055518
10.
Extracellular communication between brain cells through functional transfer of Cre mRNA.
bioRxiv
; 2023 Jan 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-36811091
11.
CRISPR-Cas9 correction of a nonsense mutation in LCA5 rescues lebercilin expression and localization in human retinal organoids.
Mol Ther Methods Clin Dev
; 29: 522-531, 2023 Jun 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-37305852
12.
Investigation of PTC124-mediated translational readthrough in a retinal organoid model of AIPL1-associated Leber congenital amaurosis.
Stem Cell Reports
; 17(10): 2187-2202, 2022 10 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-36084639
13.
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs.
Mol Ther Nucleic Acids
; 26: 432-443, 2021 Dec 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-34589289
14.
Protein Delivery of Cell-Penetrating Zinc-Finger Activators Stimulates Latent HIV-1-Infected Cells.
Mol Ther Methods Clin Dev
; 18: 145-158, 2020 Sep 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-32637446
15.
Reactivation of Latent HIV-1 Expression by Engineered TALE Transcription Factors.
PLoS One
; 11(3): e0150037, 2016.
Artigo
em Inglês
| MEDLINE | ID: mdl-26933881
16.
Erythrina mulungu alkaloids are potent inhibitors of neuronal nicotinic receptor currents in mammalian cells.
PLoS One
; 8(12): e82726, 2013.
Artigo
em Inglês
| MEDLINE | ID: mdl-24349349
17.
Altered oxygen metabolism associated to neurogenesis of induced pluripotent stem cells derived from a schizophrenic patient.
Cell Transplant
; 21(7): 1547-59, 2012.
Artigo
em Inglês
| MEDLINE | ID: mdl-21975034
18.
The magnitude of alpha7 nicotinic receptor currents in rat hippocampal neurons is dependent upon GABAergic activity and depolarization.
J Pharmacol Exp Ther
; 319(1): 376-85, 2006 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-16837558