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Lentivirus-meditated frataxin gene delivery reverses genome instability in Friedreich ataxia patient and mouse model fibroblasts.
Khonsari, H; Schneider, M; Al-Mahdawi, S; Chianea, Y G; Themis, M; Parris, C; Pook, M A; Themis, M.
Afiliação
  • Khonsari H; Division of Biosciences, Department of Life Sciences, College of Health & Life Sciences, Brunel University London, Uxbridge, Middlesex, UK.
  • Schneider M; Synthetic Biology Theme, Institute of Environment, Health & Societies, Brunel University London, Uxbridge, Middlesex, UK.
  • Al-Mahdawi S; Division of Biosciences, Department of Life Sciences, College of Health & Life Sciences, Brunel University London, Uxbridge, Middlesex, UK.
  • Chianea YG; Synthetic Biology Theme, Institute of Environment, Health & Societies, Brunel University London, Uxbridge, Middlesex, UK.
  • Themis M; Division of Biosciences, Department of Life Sciences, College of Health & Life Sciences, Brunel University London, Uxbridge, Middlesex, UK.
  • Parris C; Synthetic Biology Theme, Institute of Environment, Health & Societies, Brunel University London, Uxbridge, Middlesex, UK.
  • Pook MA; Division of Biosciences, Department of Life Sciences, College of Health & Life Sciences, Brunel University London, Uxbridge, Middlesex, UK.
  • Themis M; Synthetic Biology Theme, Institute of Environment, Health & Societies, Brunel University London, Uxbridge, Middlesex, UK.
Gene Ther ; 23(12): 846-856, 2016 12.
Article em En | MEDLINE | ID: mdl-27518705

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Ataxia de Friedreich / Terapia Genética / Proteínas de Ligação ao Ferro / Instabilidade Genômica Limite: Animals / Humans Idioma: En Revista: Gene Ther Assunto da revista: GENETICA MEDICA / TERAPEUTICA Ano de publicação: 2016 Tipo de documento: Article País de afiliação: Reino Unido

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Ataxia de Friedreich / Terapia Genética / Proteínas de Ligação ao Ferro / Instabilidade Genômica Limite: Animals / Humans Idioma: En Revista: Gene Ther Assunto da revista: GENETICA MEDICA / TERAPEUTICA Ano de publicação: 2016 Tipo de documento: Article País de afiliação: Reino Unido