Your browser doesn't support javascript.
loading
Genome editing using CRISPR-Cas9 to create the HPFH genotype in HSPCs: An approach for treating sickle cell disease and ß-thalassemia.
Ye, Lin; Wang, Jiaming; Tan, Yuting; Beyer, Ashley I; Xie, Fei; Muench, Marcus O; Kan, Yuet Wai.
Afiliação
  • Ye L; Department of Medicine, University of California, San Francisco, CA 94143; Institute for Human Genetics, University of California, San Francisco, CA 94143; yw.kan@ucsf.edu lin.ye@ucsf.edu.
  • Wang J; Department of Medicine, University of California, San Francisco, CA 94143; Institute for Human Genetics, University of California, San Francisco, CA 94143; Department of Laboratory Medicine, University of California, San Francisco, CA 94143;
  • Tan Y; Department of Medicine, University of California, San Francisco, CA 94143; State Key Laboratory of Medical Genomics, Shanghai Jiao Tong University, Shanghai 200025, China; Shanghai Institute of Hematology, Rui Jin Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai 200025, China;
  • Beyer AI; Blood Systems Research Institute, San Francisco, CA 94118.
  • Xie F; Department of Medicine, University of California, San Francisco, CA 94143; Institute for Human Genetics, University of California, San Francisco, CA 94143;
  • Muench MO; Department of Laboratory Medicine, University of California, San Francisco, CA 94143; Blood Systems Research Institute, San Francisco, CA 94118.
  • Kan YW; Department of Medicine, University of California, San Francisco, CA 94143; Institute for Human Genetics, University of California, San Francisco, CA 94143; Department of Laboratory Medicine, University of California, San Francisco, CA 94143; yw.kan@ucsf.edu lin.ye@ucsf.edu.
Proc Natl Acad Sci U S A ; 113(38): 10661-5, 2016 09 20.
Article em En | MEDLINE | ID: mdl-27601644

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Hemoglobina Fetal / Terapia Genética / Talassemia beta / Edição de Genes / Anemia Falciforme Limite: Humans Idioma: En Revista: Proc Natl Acad Sci U S A Ano de publicação: 2016 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Hemoglobina Fetal / Terapia Genética / Talassemia beta / Edição de Genes / Anemia Falciforme Limite: Humans Idioma: En Revista: Proc Natl Acad Sci U S A Ano de publicação: 2016 Tipo de documento: Article